日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

B-cell-directed CAR T-cell therapy activates CD8+ cytotoxic CARneg bystander T cells in patients and nonhuman primates

B细胞靶向CAR-T细胞疗法可激活患者和非人灵长类动物体内的CD8+细胞毒性CAR-Neg旁观者T细胞。

Kaminski, James; Fleming, Ryan A; Alvarez-Calderon, Francesca; Winschel, Marlana B; McGuckin, Connor; Ho, Emily E; Eng, Fay; Rui, Xianliang; Keskula, Paula; Cagnin, Lorenzo; Charles, Joanne; Zavistaski, Jillian; Margossian, Steven P; Kapadia, Malika A; Rottman, James B; Lane, Jennifer; Baumeister, Susanne H C; Tkachev, Victor; Shalek, Alex K; Kean, Leslie S; Gerdemann, Ulrike

Higher doses of tisagenlecleucel are associated with improved outcomes: a report from the pediatric real-world CAR consortium

较高剂量的tisagenlecleucel与更好的治疗效果相关:儿科真实世界CAR联盟的一份报告

Stefanski, Heather E; Eaton, Anne; Baggott, Christina; Rossoff, Jenna; Verneris, Michael R; Prabhu, Snehit; Pacenta, Holly L; Phillips, Christine L; Talano, Julie-An; Moskop, Amy; Margossian, Steven P; Myers, Gary Douglas; Karras, Nicole A; Brown, Patrick A; Qayed, Muna; Hermiston, Michelle; Satwani, Prakash; Krupski, M Christa; Keating, Amy K; Wilcox, Rachel; Rabik, Cara A; Fabrizio, Vanessa A; Chinnabhandar, Vasant; Goksenin, A Yasemin; Curran, Kevin J; Mackall, Crystal L; Laetsch, Theodore W; Schultz, Liora M

Disease Burden Affects Outcomes in Pediatric and Young Adult B-Cell Lymphoblastic Leukemia After Commercial Tisagenlecleucel: A Pediatric Real-World Chimeric Antigen Receptor Consortium Report

疾病负担影响儿童和青少年B细胞淋巴母细胞白血病患者接受商业化Tisagenlecleucel治疗后的预后:一项儿科真实世界嵌合抗原受体联盟报告

Schultz, Liora M; Baggott, Christina; Prabhu, Snehit; Pacenta, Holly L; Phillips, Christine L; Rossoff, Jenna; Stefanski, Heather E; Talano, Julie-An; Moskop, Amy; Margossian, Steven P; Verneris, Michael R; Myers, Gary Douglas; Karras, Nicole A; Brown, Patrick A; Qayed, Muna; Hermiston, Michelle; Satwani, Prakash; Krupski, Christa; Keating, Amy K; Wilcox, Rachel; Rabik, Cara A; Fabrizio, Vanessa A; Rouce, Rayne H; Chinnabhandar, Vasant; Kunicki, Michael; Barsan, Valentin V; Goksenin, A Yasemin; Li, Yimei; Mavroukakis, Sharon; Egeler, Emily; Curran, Kevin J; Mackall, Crystal L; Laetsch, Theodore W

Optimal fludarabine lymphodepletion is associated with improved outcomes after CAR T-cell therapy

最佳的氟达拉滨淋巴清除与CAR-T细胞疗法后疗效的改善相关。

Fabrizio, Vanessa A; Boelens, Jaap Jan; Mauguen, Audrey; Baggott, Christina; Prabhu, Snehit; Egeler, Emily; Mavroukakis, Sharon; Pacenta, Holly; Phillips, Christine L; Rossoff, Jenna; Stefanski, Heather E; Talano, Julie-An; Moskop, Amy; Margossian, Steven P; Verneris, Michael R; Myers, Gary Douglas; Karras, Nicole A; Brown, Patrick A; Qayed, Muna; Hermiston, Michelle; Satwani, Prakash; Krupski, Christa; Keating, Amy K; Wilcox, Rachel; Rabik, Cara A; Chinnabhandar, Vasant; Kunicki, Michael; Goksenin, A Yasemin; Mackall, Crystal L; Laetsch, Theodore W; Schultz, Liora M; Curran, Kevin J

Tisagenlecleucel outcomes in relapsed/refractory extramedullary ALL: a Pediatric Real World CAR Consortium Report

Tisagenlecleucel治疗复发/难治性髓外急性淋巴细胞白血病的疗效:儿科真实世界CAR联盟报告

Fabrizio, Vanessa A; Phillips, Christine L; Lane, Adam; Baggott, Christina; Prabhu, Snehit; Egeler, Emily; Mavroukakis, Sharon; Pacenta, Holly; Rossoff, Jenna; Stefanski, Heather E; Talano, Julie-An; Moskop, Amy; Margossian, Steven P; Verneris, Michael R; Myers, Gary Douglas; Karras, Nicole A; Brown, Patrick A; Qayed, Muna; Hermiston, Michelle; Satwani, Prakash; Krupski, Christa; Keating, Amy K; Wilcox, Rachel; Rabik, Cara A; Chinnabhandar, Vasant; Kunicki, Michael; Goksenin, A Yasemin; Curran, Kevin J; Mackall, Crystal L; Laetsch, Theodore W; Schultz, Liora M

Comparison of Pulmonary Toxicity after Total Body Irradiation- and Busulfan-Based Myeloablative Conditioning for Allogeneic Hematopoietic Stem Cell Transplantation in Pediatric Patients

儿童异基因造血干细胞移植中全身照射与白消安清髓预处理后肺毒性的比较

Liu, Kevin X; Poux, Nicolas; Shin, Kee-Young; Moore, Nicholas; Chen, Yu-Hui; Margossian, Steven; Whangbo, Jennifer S; Duncan, Christine N; Lehmann, Leslie E; Marcus, Karen J

Impact of Bridging Chemotherapy on Clinical Outcomes of CD19-Specific CAR T Cell Therapy in Children/Young Adults with Relapsed/Refractory B Cell Acute Lymphoblastic Leukemia

桥接化疗对复发/难治性B细胞急性淋巴细胞白血病儿童/青少年CD19特异性CAR-T细胞疗法临床疗效的影响

Shahid, Sanam; Ramaswamy, Kavitha; Flynn, Jessica; Mauguen, Audrey; Perica, Karlo; Park, Jae H; Forlenza, Christopher J; Shukla, Neerav N; Steinherz, Peter G; Margossian, Steven P; Boelens, Jaap Jan; Kernan, Nancy A; Curran, Kevin J

A multicenter study of ICU resource utilization in pediatric, adolescent and young adult patients post CAR-T therapy

一项针对接受 CAR-T 疗法的儿科、青少年和年轻成人患者 ICU 资源利用情况的多中心研究

Ragoonanan, Dristhi; Bhar, Saleh; Mohan, Gopi; Beltramo, Fernando; Khazal, Sajad J; Hurley, Caitlin; Andersen, Clark; Margossian, Steven; Neelapu, Sattva S; Shpall, Elizabeth; Gutierrez, Cristina; Tewari, Priti; Shoberu, Basirat; Talleur, Aimee; McCall, David; Nunez, Cesar; Cuglievan, Branko; Tambaro, Francesco Paolo; Petropoulos, Demetrios; Abdel-Azim, Hisham; Mahadeo, Kris M

Out-of-specification tisagenlecleucel does not compromise safety or efficacy in pediatric acute lymphoblastic leukemia

不符合规格的tisagenlecleucel不会影响儿童急性淋巴细胞白血病的安全性和有效性。

Rossoff, Jenna; Baggott, Christina; Prabhu, Snehit; Pacenta, Holly; Phillips, Christine L; Stefanski, Heather; Talano, Julie-An; Moskop, Amy; Margossian, Steven P; Verneris, Michael R; Myers, Gary Douglas; Karras, Nicole; Brown, Patrick A; Qayed, Muna; Hermiston, Michelle; Satwani, Prakash; Krupski, Christa; Keating, Amy K; Wilcox, Rachel; Rabik, Cara A; Fabrizio, Vanessa A; Kunicki, Michael; Chinnabhandar, Vasant; Goksenin, A Yasemin; Curran, Kevin J; Mackall, Crystal L; Laetsch, Theodore W; Schultz, Liora M

Risk factors for transplant-associated thrombotic microangiopathy and mortality in a pediatric cohort

儿童队列中移植相关血栓性微血管病和死亡的危险因素

Schoettler, Michelle; Lehmann, Leslie E; Margossian, Steven; Lee, Maia; Kean, Leslie S; Kao, Pei-Chi; Ma, Clement; Duncan, Christine N