Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper-IgM syndrome
细胞和造血干细胞基因编辑治疗高 IgM 综合征的建模、优化和可比疗效
期刊:EMBO Molecular Medicine
影响因子:9
doi:10.15252/emmm.202013545
Valentina Vavassori, Elisabetta Mercuri, Genni E Marcovecchio, Maria C Castiello, Giulia Schiroli, Luisa Albano, Carrie Margulies, Frank Buquicchio, Elena Fontana, Stefano Beretta, Ivan Merelli, Andrea Cappelleri, Paola Mv Rancoita, Vassilios Lougaris, Alessandro Plebani, Maria Kanariou, Arjan Lanke