日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper-IgM syndrome

细胞和造血干细胞基因编辑治疗高 IgM 综合征的建模、优化和可比疗效

Valentina Vavassori, Elisabetta Mercuri, Genni E Marcovecchio, Maria C Castiello, Giulia Schiroli, Luisa Albano, Carrie Margulies, Frank Buquicchio, Elena Fontana, Stefano Beretta, Ivan Merelli, Andrea Cappelleri, Paola Mv Rancoita, Vassilios Lougaris, Alessandro Plebani, Maria Kanariou, Arjan Lanke

Neutrophils drive type I interferon production and autoantibodies in patients with Wiskott-Aldrich syndrome

在Wiskott-Aldrich综合征患者中,中性粒细胞驱动I型干扰素的产生和自身抗体的生成。

Karla E Cervantes-Luevano ,Nicoletta Caronni ,Maria C Castiello ,Elena Fontana ,Giulia M Piperno ,Asma Naseem ,Paolo Uva ,Marita Bosticardo ,Genni E Marcovecchio ,Luigi D Notarangelo ,Maria P Cicalese ,Alessandro Aiuti ,Anna Villa ,Federica Benvenuti

Preclinical safety and efficacy of human CD34(+) cells transduced with lentiviral vector for the treatment of Wiskott-Aldrich syndrome

慢病毒载体转导人CD34(+)细胞治疗Wiskott-Aldrich综合征的临床前安全性及有效性

Samantha Scaramuzza, Luca Biasco, Anna Ripamonti, Maria C Castiello, Mariana Loperfido, Elena Draghici, Raisa J Hernandez, Fabrizio Benedicenti, Marina Radrizzani, Monica Salomoni, Marco Ranzani, Cynthia C Bartholomae, Elisa Vicenzi, Andrea Finocchi, Robbert Bredius, Marita Bosticardo, Manfred Schmi