AAVrh10 Gene Therapy Ameliorates Central and Peripheral Nervous System Disease in Canine Globoid Cell Leukodystrophy (Krabbe Disease)
AAVrh10 基因疗法改善犬球状细胞白质营养不良症(克拉伯病)的中枢和周围神经系统疾病
期刊:Human Gene Therapy
影响因子:3.9
doi:10.1089/hum.2017.151
Allison M Bradbury, Mohammed A Rafi, Jessica H Bagel, Becky K Brisson, Michael S Marshall, Jill Pesayco Salvador, Xuntain Jiang, Gary P Swain, Maria L Prociuk, Patricia A ODonnell, Caitlin Fitzgerald, Daniel S Ory, Ernesto R Bongarzone, G Diane Shelton, David A Wenger, Charles H Vite