Creation of de novo cryptic splicing for ALS/FTD precision medicine
为 ALS/FTD 精准医疗创建从头隐蔽剪接
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doi:10.1101/2023.11.15.565967
Oscar G Wilkins, Max Z Y J Chien, Josette J Wlaschin, Maria Pisliakova, David Thompson, Holly Digby, Rebecca L Simkin, Juan Antinao Diaz, Puja R Mehta, Matthew J Keuss, Matteo Zanovello, Anna-Leigh Brown, Peter Harley, Annalucia Darbey, Rajvinder Karda, Elizabeth M C Fisher, Tom J Cunningham, Claire