Nusinersen Modulates Proteomics Profiles of Cerebrospinal Fluid in Spinal Muscular Atrophy Type 1 Patients
Nusinersen 调节脊髓性肌萎缩症 1 型患者的脑脊液蛋白质组学特征
期刊:International Journal of Molecular Sciences
影响因子:0.7
doi:10.3390/ijms22094329
Laura Bianchi, Maria Sframeli, Lorenza Vantaggiato, Gian Luca Vita, Annamaria Ciranni, Francesca Polito, Rosaria Oteri, Eloisa Gitto, Fabrizio Di Giuseppe, Stefania Angelucci, Antonio Versaci, Sonia Messina, Giuseppe Vita, Luca Bini, M'hammed Aguennouz