日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Context base editing for splice correction of IVSI-110 β-thalassemia

用于 IVSI-110 β-地中海贫血剪接校正的上下文库编辑

Basma Naiisseh, Panayiota L Papasavva, Nikoletta Y Papaioannou, Marios Tomazou, Lola Koniali, Xenia Felekis, Constantina G Constantinou, Maria Sitarou, Soteroula Christou, Marina Kleanthous, Carsten W Lederer, Petros Patsali

Evaluation of Mono- and Bi-Functional GLOBE-Based Vectors for Therapy of β-Thalassemia by HBBAS3 Gene Addition and Mutation-Specific RNA Interference

通过 HBBAS3 基因添加和突变特异性 RNA 干扰对 β-地中海贫血进行治疗的单体和双功能 GLOBE 载体的评估

Lola Koniali, Christina Flouri, Markela I Kostopoulou, Nikoletta Y Papaioannou, Panayiota L Papasavva, Basma Naiisseh, Coralea Stephanou, Anthi Demetriadou, Maria Sitarou, Soteroula Christou, Michael N Antoniou, Marina Kleanthous, Petros Patsali, Carsten W Lederer

High-efficiency editing in hematopoietic stem cells and the HUDEP-2 cell line based on in vitro mRNA synthesis

基于体外 mRNA 合成的造血干细胞和 HUDEP-2 细胞系高效编辑

Nikoletta Y Papaioannou, Petros Patsali, Basma Naiisseh, Panayiota L Papasavva, Lola Koniali, Ryo Kurita, Yukio Nakamura, Soteroula Christou, Maria Sitarou, Claudio Mussolino, Toni Cathomen, Marina Kleanthous, Carsten W Lederer

Distinct miRNA Signatures and Networks Discern Fetal from Adult Erythroid Differentiation and Primary from Immortalized Erythroid Cells

独特的 miRNA 特征和网络可辨别胎儿红细胞与成人红细胞的分化以及原代红细胞与永生化红细胞

Panayiota L Papasavva, Nikoletta Y Papaioannou, Petros Patsali, Ryo Kurita, Yukio Nakamura, Maria Sitarou, Soteroulla Christou, Marina Kleanthous, Carsten W Lederer

Relative and Absolute Quantification of Aberrant and Normal Splice Variants in HBBIVSI-110 (G > A) β-Thalassemia

HBBIVSI-110 (G > A) β-地中海贫血中异常和正常剪接变体的相对和绝对定量

Petros Patsali, Panayiota Papasavva, Soteroulla Christou, Maria Sitarou, Michael N Antoniou, Carsten W Lederer, Marina Kleanthous

A novel mutation in the erythroid transcription factor KLF1 is likely responsible for ameliorating β-thalassemia major

红细胞转录因子 KLF1 的新突变可能有助于改善重型 β 地中海贫血

Pavlos Fanis, Ioanna Kousiappa, Marios Phylactides, Andreani Kyrri, Michael Hadjigavriel, Soteroula Christou, Maria Sitarou, Marina Kleanthous

The Scope for Thalassemia Gene Therapy by Disruption of Aberrant Regulatory Elements

通过破坏异常调控元件进行地中海贫血基因治疗的范围

Petros Patsali, Claudio Mussolino, Petros Ladas, Argyro Floga, Annita Kolnagou, Soteroula Christou, Maria Sitarou, Michael N Antoniou, Toni Cathomen, Carsten Werner Lederer, Marina Kleanthous

Rapid and Sensitive Assessment of Globin Chains for Gene and Cell Therapy of Hemoglobinopathies

对血红蛋白病基因和细胞治疗的珠蛋白链进行快速灵敏的评估

Constantinos C Loucari, Petros Patsali, Thamar B van Dijk, Coralea Stephanou, Panayiota Papasavva, Maria Zanti, Ryo Kurita, Yukio Nakamura, Soteroulla Christou, Maria Sitarou, Sjaak Philipsen, Carsten W Lederer, Marina Kleanthous