Genome editing in mitochondria corrects a pathogenic mtDNA mutation in vivo
线粒体基因组编辑可纠正体内致病的线粒体DNA突变
期刊:Nature Medicine
影响因子:58.7
doi:10.1038/s41591-018-0165-9
Payam A Gammage, Carlo Viscomi, Marie-Lune Simard, Ana S H Costa, Edoardo Gaude, Christopher A Powell, Lindsey Van Haute, Beverly J McCann, Pedro Rebelo-Guiomar, Raffaele Cerutti, Lei Zhang, Edward J Rebar, Massimo Zeviani, Christian Frezza, James B Stewart, Michal Minczuk