日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Effective targeting of PDGFRA-altered high-grade glioma with avapritinib

avapritinib 可有效靶向治疗 PDGFRA 改变的高级别胶质瘤

Lisa Mayr ,Sina Neyazi ,Kallen Schwark ,Maria Trissal ,Alexander Beck ,Jenna Labelle ,Sebastian K Eder ,Liesa Weiler-Wichtl ,Joana G Marques ,Carlos A O de Biagi-Junior ,Costanza Lo Cascio ,Owen Chapman ,Sunita Sridhar ,Rishaan Kenkre ,Aditi Dutta ,Shanqing Wang ,Jessica Wang ,Olivia Hack ,Andrezza Nascimento ,Cuong M Nguyen ,Sophia Castellani ,Jacob S Rozowsky ,Andrew Groves ,Eshini Panditharatna ,Gustavo Alencastro Veiga Cruzeiro ,Rebecca D Haase ,Kuscha Tabatabai ,Sibylle Madlener ,Jack Wadden ,Tiffany Adam ,Seongbae Kong ,Madeline Miclea ,Tirth Patel ,Katharina Bruckner ,Daniel Senfter ,Anna Lämmerer ,Jeffrey Supko ,Armin S Guntner ,Hana Palova ,Jakub Neradil ,Natalia Stepien ,Daniela Lötsch-Gojo ,Walter Berger ,Ulrike Leiss ,Verena Rosenmayr ,Christian Dorfer ,Karin Dieckmann ,Andreas Peyrl ,Amedeo A Azizi ,Alicia Baumgartner ,Ondrej Slaby ,Petra Pokorna ,Louise M Clark ,Amy Cameron ,Quang-De Nguyen ,Hiroaki Wakimoto ,Frank Dubois ,Noah F Greenwald ,Pratiti Bandopadhayay ,Rameen Beroukhim ,Keith Ligon ,Christof Kramm ,Annika Bronsema ,Simon Bailey ,Ana Guerreiro Stucklin ,Sabine Mueller ,Mary Skrypek ,Nina Martinez ,Daniel C Bowers ,David T W Jones ,Chris Jones ,Natalie Jäger ,Jaroslav Sterba ,Leonhard Müllauer ,Christine Haberler ,Chandan Kumar-Sinha ,Arul Chinnaiyan ,Rajen Mody ,Lukas Chavez ,Julia Furtner ,Carl Koschmann ,Johannes Gojo ,Mariella G Filbin

Dissecting the immune landscape in pediatric high-grade glioma reveals cell state changes under therapeutic pressure

剖析儿童高级别胶质瘤的免疫微环境,揭示治疗压力下的细胞状态变化

Jenna J LaBelle,Rebecca D Haase,Alexander Beck,Jacob Haase,Li Jiang,Carlos Alberto Oliveira de Biagi Jr,Sina Neyazi,Bernhard Englinger,Ilon Liu,Maria Trissal,Daeun Jeong,Olivia A Hack,Andrezza Nascimento,McKenzie L Shaw,Cuong M Nguyen,Sophia Castellani,Nathan D Mathewson,Orr Ashenberg,Gustavo Alencastro Veiga Cruzeiro,Tom Rosenberg,Jayne R Vogelzang,Jason Pyrdol,Sascha Marx,Adrienne M Luomo,Anze Godicelj,Alicia Baumgartner,Jacob S Rozowsky,Sibylle Madlener,Lisa Mayr,Andreas Peyrl,Rene Geyeregger,Daniela Loetsch,Christian Dorfer,Christine Haberler,Natalia Stepien,Irene Slavc,Tom Belle Davidson,Robert M Prins,Kee Kiat Yeo,Tabitha Cooney,Keith Ligon,Hart Lidov,Sanda Alexandrescu,Lissa C Baird,Johannes Gojo,Kai W Wucherpfennig,Mariella G Filbin

GABAergic neuronal lineage development determines clinically actionable targets in diffuse hemispheric glioma, H3G34-mutant

GABA能神经元谱系发育决定了弥漫性半球胶质瘤(H3G34突变型)中具有临床意义的靶点

Ilon Liu ,Gustavo Alencastro Veiga Cruzeiro ,Lynn Bjerke ,Rebecca F Rogers ,Yura Grabovska ,Alexander Beck ,Alan Mackay ,Tara Barron ,Olivia A Hack ,Michael A Quezada ,Valeria Molinari ,McKenzie L Shaw ,Marta Perez-Somarriba ,Sara Temelso ,Florence Raynaud ,Ruth Ruddle ,Eshini Panditharatna ,Bernhard Englinger ,Hafsa M Mire ,Li Jiang ,Andrezza Nascimento ,Jenna LaBelle ,Rebecca Haase ,Jacob Rozowsky ,Sina Neyazi ,Alicia-Christina Baumgartner ,Sophia Castellani ,Samantha E Hoffman ,Amy Cameron ,Murry Morrow ,Quang-De Nguyen ,Giulia Pericoli ,Sibylle Madlener ,Lisa Mayr ,Christian Dorfer ,Rene Geyeregger ,Christopher Rota ,Gerda Ricken ,Keith L Ligon ,Sanda Alexandrescu ,Rodrigo T Cartaxo ,Benison Lau ,Santhosh Uphadhyaya ,Carl Koschmann ,Emelie Braun ,Miri Danan-Gotthold ,Lijuan Hu ,Kimberly Siletti ,Erik Sundström ,Rebecca Hodge ,Ed Lein ,Sameer Agnihotri ,David D Eisenstat ,Simon Stapleton ,Andrew King ,Cristina Bleil ,Angela Mastronuzzi ,Kristina A Cole ,Angela J Waanders ,Angel Montero Carcaboso ,Ulrich Schüller ,Darren Hargrave ,Maria Vinci ,Fernando Carceller ,Christine Haberler ,Irene Slavc ,Sten Linnarsson ,Johannes Gojo ,Michelle Monje ,Chris Jones ,Mariella G Filbin

Multi-omics approaches reveal that diffuse midline gliomas present altered DNA replication and are susceptible to replication stress therapy

多组学方法表明,弥漫性中线胶质瘤表现出 DNA 复制改变,且易受复制应激疗法的影响

Anastasia E Hains, Kashish Chetal, Tsunetoshi Nakatani, Joana G Marques, Andreas Ettinger, Carlos A O Biagi Junior, Adriana Gonzalez-Sandoval, Renjitha Pillai, Mariella G Filbin, Maria-Elena Torres-Padilla, Ruslan I Sadreyev, Capucine Van Rechem

TIM-3 blockade in diffuse intrinsic pontine glioma models promotes tumor regression and antitumor immune memory

在弥漫性内生性脑桥胶质瘤模型中,TIM-3阻断可促进肿瘤消退和抗肿瘤免疫记忆。

Iker Ausejo-Mauleon ,Sara Labiano ,Daniel de la Nava ,Virginia Laspidea ,Marta Zalacain ,Lucía Marrodán ,Marc García-Moure ,Marisol González-Huarriz ,Irati Hervás-Corpión ,Laasya Dhandapani ,Silvestre Vicent ,Maria Collantes ,Iván Peñuelas ,Oren J Becher ,Mariella G Filbin ,Li Jiang ,Jenna Labelle ,Carlos A O de Biagi-Junior ,Javad Nazarian ,Sandra Laternser ,Timothy N Phoenix ,Jasper van der Lugt ,Mariette Kranendonk ,Raoull Hoogendijk ,Sabine Mueller ,Carlos De Andrea ,Ana C Anderson ,Elizabeth Guruceaga ,Carl Koschmann ,Viveka Nand Yadav ,Jaime Gállego Pérez-Larraya ,Ana Patiño-García ,Fernando Pastor ,Marta M Alonso

Clinical Efficacy of ONC201 in H3K27M-Mutant Diffuse Midline Gliomas Is Driven by Disruption of Integrated Metabolic and Epigenetic Pathways

ONC201治疗H3K27M突变型弥漫性中线胶质瘤的临床疗效是由整合代谢和表观遗传通路紊乱驱动的

Sriram Venneti # ,Abed Rahman Kawakibi # ,Sunjong Ji # ,Sebastian M Waszak # ,Stefan R Sweha # ,Mateus Mota # ,Matthew Pun # ,Akash Deogharkar ,Chan Chung ,Rohinton S Tarapore ,Samuel Ramage ,Andrew Chi ,Patrick Y Wen ,Isabel Arrillaga-Romany ,Tracy T Batchelor ,Nicholas A Butowski ,Ashley Sumrall ,Nicole Shonka ,Rebecca A Harrison ,John de Groot ,Minesh Mehta ,Matthew D Hall ,Doured Daghistani ,Timothy F Cloughesy ,Benjamin M Ellingson ,Kevin Beccaria ,Pascale Varlet ,Michelle M Kim ,Yoshie Umemura ,Hugh Garton ,Andrea Franson ,Jonathan Schwartz ,Rajan Jain ,Maureen Kachman ,Heidi Baum ,Charles F Burant ,Sophie L Mottl ,Rodrigo T Cartaxo ,Vishal John ,Dana Messinger ,Tingting Qin ,Erik Peterson ,Peter Sajjakulnukit ,Karthik Ravi ,Alyssa Waugh ,Dustin Walling ,Yujie Ding ,Ziyun Xia ,Anna Schwendeman ,Debra Hawes ,Fusheng Yang ,Alexander R Judkins ,Daniel Wahl ,Costas A Lyssiotis ,Daniel de la Nava ,Marta M Alonso ,Augustine Eze ,Jasper Spitzer ,Susanne V Schmidt ,Ryan J Duchatel ,Matthew D Dun ,Jason E Cain ,Li Jiang ,Sylwia A Stopka ,Gerard Baquer ,Michael S Regan ,Mariella G Filbin ,Nathalie Y R Agar ,Lili Zhao ,Chandan Kumar-Sinha ,Rajen Mody ,Arul Chinnaiyan ,Ryo Kurokawa ,Drew Pratt ,Viveka N Yadav ,Jacques Grill ,Cassie Kline ,Sabine Mueller ,Adam Resnick ,Javad Nazarian ,Joshua E Allen ,Yazmin Odia ,Sharon L Gardner ,Carl Koschmann

A druggable addiction to de novo pyrimidine biosynthesis in diffuse midline glioma

弥漫性中线胶质瘤中对从头嘧啶生物合成的可药物依赖性

Sharmistha Pal ,Jakub P Kaplan ,Huy Nguyen ,Sylwia A Stopka ,Milan R Savani ,Michael S Regan ,Quang-De Nguyen ,Kristen L Jones ,Lisa A Moreau ,Jingyu Peng ,Marina G Dipiazza ,Andrew J Perciaccante ,Xiaoting Zhu ,Bradley R Hunsel ,Kevin X Liu ,Sanda Alexandrescu ,Rachid Drissi ,Mariella G Filbin ,Samuel K McBrayer ,Nathalie Y R Agar ,Dipanjan Chowdhury ,Daphne A Haas-Kogan

The landscape of tumor cell states and spatial organization in H3-K27M mutant diffuse midline glioma across age and location

H3-K27M突变型弥漫性中线胶质瘤在不同年龄和部位的肿瘤细胞状态和空间组织结构

Ilon Liu # ,Li Jiang # ,Erik R Samuelsson # ,Sergio Marco Salas ,Alexander Beck ,Olivia A Hack ,Daeun Jeong ,McKenzie L Shaw ,Bernhard Englinger ,Jenna LaBelle ,Hafsa M Mire ,Sibylle Madlener ,Lisa Mayr ,Michael A Quezada ,Maria Trissal ,Eshini Panditharatna ,Kati J Ernst ,Jayne Vogelzang ,Taylor A Gatesman ,Matthew E Halbert ,Hana Palova ,Petra Pokorna ,Jaroslav Sterba ,Ondrej Slaby ,Rene Geyeregger ,Aaron Diaz ,Izac J Findlay ,Matthew D Dun ,Adam Resnick ,Mario L Suvà ,David T W Jones ,Sameer Agnihotri ,Jessica Svedlund ,Carl Koschmann ,Christine Haberler ,Thomas Czech ,Irene Slavc ,Jennifer A Cotter ,Keith L Ligon ,Sanda Alexandrescu ,W K Alfred Yung ,Isabel Arrillaga-Romany ,Johannes Gojo ,Michelle Monje ,Mats Nilsson ,Mariella G Filbin

BAF Complex Maintains Glioma Stem Cells in Pediatric H3K27M Glioma

BAF复合物在儿童H3K27M胶质瘤中维持胶质瘤干细胞

Eshini Panditharatna # ,Joana G Marques # ,Tingjian Wang ,Maria C Trissal ,Ilon Liu ,Li Jiang ,Alexander Beck ,Andrew Groves ,Neekesh V Dharia ,Deyao Li ,Samantha E Hoffman ,Guillaume Kugener ,McKenzie L Shaw ,Hafsa M Mire ,Olivia A Hack ,Joshua M Dempster ,Caleb Lareau ,Lingling Dai ,Logan H Sigua ,Michael A Quezada ,Ann-Catherine J Stanton ,Meghan Wyatt ,Zohra Kalani ,Amy Goodale ,Francisca Vazquez ,Federica Piccioni ,John G Doench ,David E Root ,Jamie N Anastas ,Kristen L Jones ,Amy Saur Conway ,Sylwia Stopka ,Michael S Regan ,Yu Liang ,Hyuk-Soo Seo ,Kijun Song ,Puspalata Bashyal ,William P Jerome ,Nathan D Mathewson ,Sirano Dhe-Paganon ,Mario L Suvà ,Angel M Carcaboso ,Cinzia Lavarino ,Jaume Mora ,Quang-De Nguyen ,Keith L Ligon ,Yang Shi ,Sameer Agnihotri ,Nathalie Y R Agar ,Kimberly Stegmaier ,Charles D Stiles ,Michelle Monje ,Todd R Golub ,Jun Qi ,Mariella G Filbin

Resolving medulloblastoma cellular architecture by single-cell genomics

通过单细胞基因组学解析髓母细胞瘤细胞结构

Volker Hovestadt #, Kyle S Smith #, Laure Bihannic #, Mariella G Filbin #, McKenzie L Shaw, Alicia Baumgartner, John C DeWitt, Andrew Groves, Lisa Mayr, Hannah R Weisman, Alyssa R Richman, Marni E Shore, Liliana Goumnerova, Celeste Rosencrance, Robert A Carter, Timothy N Phoenix, Jennifer L Hadley,