Ryanodine channel complex stabilizer compound S48168/ARM210 as a disease modifier in dystrophin-deficient mdx mice: proof-of-concept study and independent validation of efficacy
瑞安诺丁通道复合稳定剂 S48168/ARM210 作为肌营养不良症 mdx 小鼠的疾病调节剂:概念验证研究和独立功效验证
期刊:FASEB Journal
影响因子:4.4
doi:10.1096/fj.201700182RRR
Roberta Francesca Capogrosso, Paola Mantuano, Kitipong Uaesoontrachoon, Anna Cozzoli, Arcangela Giustino, Todd Dow, Sadish Srinivassane, Marina Filipovic, Christina Bell, Jack Vandermeulen, Ada Maria Massari, Michela De Bellis, Elena Conte, Sabata Pierno, Giulia Maria Camerino, Antonella Liantonio,