A novel glucosylceramide synthase inhibitor attenuates alpha synuclein pathology and lysosomal dysfunction in preclinical models of synucleinopathy
一种新型葡萄糖神经酰胺合酶抑制剂可减轻突触核蛋白病临床前模型中的 α 突触核蛋白病理和溶酶体功能障碍
期刊:Neurobiology of Disease
影响因子:5.1
doi:10.1016/j.nbd.2021.105507
Mali Cosden, Sarah Jinn, Lihang Yao, Cheryl A Gretzula, Monika Kandebo, Dawn Toolan, Nathan G Hatcher, Lei Ma, Wei Lemaire, Gregory C Adam, Christine Burlein, Christina Minnick, Rose Flick, Marla L Watt, James Mulhearn, Mark Fraley, Robert E Drolet, Jacob N Marcus, Sean M Smith