Retention of lysosomal acid sphingomyelinase protects from Niemann-Pick Disease
溶酶体酸性鞘磷脂酶的保留可预防尼曼-匹克病
期刊:Neurobiology of Disease
影响因子:5.6
doi:10.1016/j.nbd.2025.107147
Beard, Cameron A; Hermanson, Kyra N; Snider, Justin M; Hara, Aki; Dahl, Brandon K; Allopenna, Janet J; Marron, Marilyn T; Newcomb, Benjamin; Low, Benjamin E; Wiles, Michael V; Jenkins, Russell W; Obeid, Lina M; Hannun, Yusuf A; Snider, Ashley J