Potent spinal parenchymal AAV9-mediated gene delivery by subpial injection in adult rats and pigs
通过皮下注射将AAV9介导的基因高效递送至成年大鼠和猪的脊髓实质
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1038/mtm.2016.46
Miyanohara, Atsushi; Kamizato, Kota; Juhas, Stefan; Juhasova, Jana; Navarro, Michael; Marsala, Silvia; Lukacova, Nada; Hruska-Plochan, Marian; Curtis, Erik; Gabel, Brandon; Ciacci, Joseph; Ahrens, Eric T; Kaspar, Brian K; Cleveland, Don; Marsala, Martin