Data from the European registry for patients with McArdle disease (EUROMAC): functional status and social participation
来自欧洲麦卡德尔病患者登记处(EUROMAC)的数据:功能状态和社会参与
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-023-02825-z
Karazi, Walaa; Scalco, Renata S; Stemmerik, Mads G; Løkken, Nicoline; Lucia, Alejandro; Santalla, Alfredo; Martinuzzi, Andrea; Vavla, Marinela; Reni, Gianluigi; Toscano, Antonio; Musumeci, Olimpia; Kouwenberg, Carlyn V; Laforêt, Pascal; Millán, Beatriz San; Vieitez, Irene; Siciliano, Gabriele; Kühnle, Enrico; Trost, Rebecca; Sacconi, Sabrina; Durmus, Hacer; Kierdaszuk, Biruta; Wakelin, Andrew; Andreu, Antoni L; Pinós, Tomàs; Marti, Ramon; Quinlivan, Ros; Vissing, John; Voermans, Nicol C