Selection-free genome editing of the sickle mutation in human adult hematopoietic stem/progenitor cells
无需选择即可对人类成体造血干/祖细胞中的镰状细胞突变进行基因组编辑
期刊:Science Translational Medicine
影响因子:14.6
doi:10.1126/scitranslmed.aaf9336
DeWitt, Mark A; Magis, Wendy; Bray, Nicolas L; Wang, Tianjiao; Berman, Jennifer R; Urbinati, Fabrizia; Heo, Seok-Jin; Mitros, Therese; Muñoz, Denise P; Boffelli, Dario; Kohn, Donald B; Walters, Mark C; Carroll, Dana; Martin, David I K; Corn, Jacob E