An antisense oligonucleotide-based strategy to ameliorate cognitive dysfunction in the 22q11.2 Deletion Syndrome
一种基于反义寡核苷酸的策略,用于改善22q11.2缺失综合征的认知功能障碍
期刊:Elife
影响因子:6.4
doi:10.7554/eLife.103328
Pratibha Thakur # ,Martin Lackinger # ,Anastasia Diamantopoulou ,Sneha Rao ,Yijing Chen ,Khakima Khalizova ,Annie Ferng ,Curt Mazur ,Holly Kordasiewicz ,Robert J Shprintzen ,Sander Markx ,Bin Xu ,Joseph A Gogos