Toward RNAi therapy for the polyglutamine disease Machado-Joseph disease.
针对多聚谷氨酰胺疾病 Machado-Joseph 病的 RNAi 疗法
期刊:Molecular Therapy
影响因子:12
doi:10.1038/mt.2013.144
Costa Maria do Carmo, Luna-Cancalon Katiuska, Fischer Svetlana, Ashraf Naila S, Ouyang Michelle, Dharia Rahil M, Martin-Fishman Lucas, Yang Yemen, Shakkottai Vikram G, Davidson Beverly L, RodrÃguez-Lebrón Edgardo, Paulson Henry L