S106: LONG-TERM FOLLOW-UP OF BETA-THALASSEMIA PATIENTS TREATED WITH HEMATOPOIETIC STEM CELL GENE THERAPY
S106:接受造血干细胞基因治疗的β-地中海贫血患者的长期随访
期刊:Scientific Reports
影响因子:3.9
doi:10.1038/s41598-024-84225-2
Cherie, Negesse; Deress, Teshiwal; Wolde, Maereg; Teketelew, Bisrat; Tamir, Mebratu; Angelo, Abiy; Terekegne, Amare Mekuanint; Chane, Elias; Nigus, Mesele; Berta, Dereje Mengesha; Adane, Kasaw; Donato, Elisa; Correia, Nadia; Andresen, Carolin; Karpova, Darja; Würth, Roberto; Klein, Corinna; Sohn, Markus; Przybylla, Adriana; Zeisberger, Petra; Rothfelder, Kathrin; Salih, Helmut; Bonig, Halvard; Stasik, Sebastian; Röllig, Christoph; Dolnik, Anna; Bullinger, Lars; Buchholz, Frank; Thiede, Christian; Hübschmann, Daniel; Trumpp, Andreas; Głodkowska-Mrówka, Eliza; Cieloch, Adrianna; Manda-Handzlik, Aneta; Rams, Anna; Wołowiec, Magdalena; Laguna, Pawel; Mrowka, Piotr; Ambaglio, C; Benatti, S V; Tartari, C J; Giaccherini, C; Russo, L; Marchetti, M; Palladino, A M; Schieppati, F; Venturelli, S; Barcella, L; Rizzi, M; Falanga, A; Marktel, S; Scaramuzza, S; Giglio, F; Cicalese, M; Lidonnici, M; Rossi, C; Calbi, V; Masera, N; D’Angelo, E; Mirra, N; Origa, R; Tartaglione, I; Perrotta, S; Viarengo, G; Santoleri, L; Milani, R; Gattillo, S; Calabria, A; Montini, E; Graziadei, G; Naldini, L; Cappellini, M; Aiuti, A; Ciceri, F; Ferrari, G
干细胞
发育与干细胞
细胞基因治疗
贫血
基因治疗
代谢
细胞生物学