日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Preclinical lentiviral hematopoietic stem cell gene therapy corrects Pompe disease-related muscle and neurological manifestations.

临床前慢病毒造血干细胞基因疗法可纠正庞贝病相关的肌肉和神经系统症状

Yoon John K, Schindler Jeffrey W, Loperfido Mariana, Baricordi Cristina, DeAndrade Mark P, Jacobs Mary E, Treleaven Christopher, Plasschaert Robert N, Yan Aimin, Barese Cecilia N, Dogan Yildirim, Chen Vicky Ping, Fiorini Claudia, Hull Fritz, Barbarossa Luigi, Unnisa Zeenath, Ivanov Daniel, Kutner Robert H, Guda Swaroopa, Oborski Christine, Maiwald Tim, Michaud Véronique, Rothe Michael, Schambach Axel, Pfeifer Richard, Mason Chris, Biasco Luca, van Til Niek P

Engineering an Autonucleolytic Mammalian Suspension Host Cell Line to Reduce DNA Impurity Levels in Serum-Free Lentiviral Process Streams

构建自核酸酶哺乳动物悬浮宿主细胞系以降低无血清慢病毒工艺流程中的DNA杂质水平

Howe, Geoffrey; Wasmuth, Matthew; Emanuelle, Pamela; Massaro, Giulia; Rahim, Ahad A; Ali, Sadfer; Rivera, Milena; Ward, John; Keshavarz-Moore, Eli; Mason, Chris; Nesbeth, Darren N

Trimethoprim-sulfamethoxazole acute respiratory distress syndrome requiring lung transplantation

甲氧苄啶-磺胺甲噁唑引起的急性呼吸窘迫综合征需要肺移植

Donnan, Matthew; Siemienowicz, Miranda; Tay, Hui Sien; McLean, Catriona; Philpot, Steve; Mason, Chris; Snell, Greg; Glaspole, Ian; Stirling, Rob G

2835. Utilization of Clinical-Grade Metagenomics in Urinary Tract Infection Diagnostics: Improving High-Risk Patients’ Outcomes with a Genomic-Based Assay

2835. 临床级宏基因组学在泌尿道感染诊断中的应用:利用基于基因组的检测方法改善高危患者的预后

Mukuhlani, Blessed T; Romero, Eduardo J Morfa; Augenbraun, Michael; Rivera, Tiara; Rey, Sol; Serrano, Xavier O Jirau; Papciak, John C; Patel, Suraj S; Harrison, Bridget; Plourde, Anna; Otto, Caitlin; Mason, Chris; Wells, Heather L; Danko, David C; O’Hara, Niamh B; Couto-Rodriguez, Mara; Nagy-Szakal, Dorottya

Gene Therapy Developments for Pompe Disease

庞贝氏症基因治疗进展

Unnisa, Zeenath; Yoon, John K; Schindler, Jeffrey W; Mason, Chris; van Til, Niek P

DNA methylation landscapes of 1538 breast cancers reveal a replication-linked clock, epigenomic instability and cis-regulation

1538例乳腺癌的DNA甲基化图谱揭示了与复制相关的生物钟、表观基因组不稳定性以及顺式调控

Batra, Rajbir Nath; Lifshitz, Aviezer; Vidakovic, Ana Tufegdzic; Chin, Suet-Feung; Sati-Batra, Ankita; Sammut, Stephen-John; Provenzano, Elena; Ali, H Raza; Dariush, Ali; Bruna, Alejandra; Murphy, Leigh; Purushotham, Arnie; Ellis, Ian; Green, Andrew; Garrett-Bakelman, Francine E; Mason, Chris; Melnick, Ari; Aparicio, Samuel A J R; Rueda, Oscar M; Tanay, Amos; Caldas, Carlos

The 3Rs of Cell Therapy

细胞疗法的3R原则

Caplan, Arnold I; Mason, Chris; Reeve, Brock

Cost of Stem Cell-Based Tissue-Engineered Airway Transplants in the United Kingdom: Case Series

英国基于干细胞的组织工程气道移植的成本:病例系列

Culme-Seymour, Emily J; Mason, Katrina; Vallejo-Torres, Laura; Carvalho, Carla; Partington, Leanne; Crowley, Claire; Hamilton, Nick J; Toll, Ed C; Butler, Colin R; Elliott, Martin J; Birchall, Martin A; Lowdell, Mark W; Mason, Chris

Mutational cooperativity linked to combinatorial epigenetic gain of function in acute myeloid leukemia

急性髓系白血病中与组合表观遗传功能获得相关的突变协同性

Shih, Alan H; Jiang, Yanwen; Meydan, Cem; Shank, Kaitlyn; Pandey, Suveg; Barreyro, Laura; Antony-Debre, Ileana; Viale, Agnes; Socci, Nicholas; Sun, Yongming; Robertson, Alexander; Cavatore, Magali; de Stanchina, Elisa; Hricik, Todd; Rapaport, Franck; Woods, Brittany; Wei, Chen; Hatlen, Megan; Baljevic, Muhamed; Nimer, Stephen D; Tallman, Martin; Paietta, Elisabeth; Cimmino, Luisa; Aifantis, Iannis; Steidl, Ulrich; Mason, Chris; Melnick, Ari; Levine, Ross L

Cells: from Robert Hooke to cell therapy--a 350 year journey

细胞:从罗伯特·胡克到细胞疗法——350年的历程

Hyllner, Johan; Mason, Chris; Wilmut, Ian