Efficacy and safety of avatrombopag in combination with immunosuppressive therapy in treatment-naïve and relapsed/refractory severe aplastic anaemia: protocol for the DIAAMOND-Ava-FIRST and DIAAMOND-Ava-NEXT Bayesian Optimal Phase II trials
阿伐曲波帕联合免疫抑制疗法治疗初治和复发/难治性重型再生障碍性贫血的疗效和安全性:DIAAMOND-Ava-FIRST 和 DIAAMOND-Ava-NEXT 贝叶斯最优 II 期试验方案
期刊:BMJ Open
影响因子:2.3
doi:10.1136/bmjopen-2023-076246
McQuilten, Zoe; Heritier, Stephane; Fox, Lucy; Fox, Vanessa; Young, Lauren; Blombery, Piers; Cunningham, Ilona; Curnow, Jennifer; Higgins, Alisa; Hiwase, Devendra K; Filshie, Robin; Firkin, Frank; Lacaze, Paul; Mason, Kylie; Mills, Anthony K; Pepperell, Dominic; Patil, Sushrut; Stevenson, William; Szer, Jeff; Waters, Neil; Wilson, Kate; Ting, Stephen; Wood, Erica