日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Increased intervals in enzyme replacement therapy for stable type 1 Gaucher disease: A non-inferiority sequential trial emulation

延长酶替代疗法治疗稳定型1型戈谢病的间隔时间:一项非劣效性序贯试验模拟研究

Beydon, Maxime; Stirnemann, Jérôme; Yousfi, Karima; Zebiche, Samira; Hamroun, Dalil; Brassier, Anaïs; Pichard, Samia; Swiader, Laure; de Villemeur, Thierry Billette; Héron, Bénédicte; Dalbies, Florence; Cador, Bérengère; Guemann, Anne-Sophie; Gaches, Francis; Hivert, Bénédicte; Leguy-Seguin, Vanessa; Masseau, Agathe; Pers, Yves-Marie; Pettazzoni, Magali; Bekri, Soumeya; Caillaud, Catherine; Guillou, Edouard Le; Szymanowski, Marie; Astudillo, Leonardo; Mauhin, Wladimir; Nadjar, Yann; Serratrice, Christine; Berger, Marc G; Camou, Fabrice; Belmatoug, Nadia; Nguyen, Yann

Treatment-related benefit and satisfaction in patients with Fabry disease in France: insight into patients' expectations and preferences from the prospective, non-interventional SATIS-Fab study

法国法布里病患者的治疗获益和满意度:来自前瞻性、非干预性 SATIS-Fab 研究的患者期望和偏好分析

Lidove, Olivier; Masseau, Agathe; Pugnet, Grégory; Lacombe, Didier; Dussol, Bertrand; Bekri, Soumeya; Hagège, Albert; Martinez, Caroline; Fardini, Yann; Fouilhoux, Alain; Noël, Esther

A multidisciplinary diagnostic approach to pulmonary fibrosis in dogs and cats

犬猫肺纤维化的多学科诊断方法

Reinero, Carol R; Masseau, Isabelle; Williams, Kurt J

Epidemiology of Gaucher Disease in France: Trends in Incidence, Mortality, Management, and Complications Over Three Decades

法国戈谢病流行病学:三十年来的发病率、死亡率、治疗和并发症趋势

Nguyen, Yann; Beydon, Maxime; Yousfi, Karima; Zebiche, Samira; Hamroun, Dalil; Brassier, Anaïs; Pichard, Samia; Swiader, Laure; Billette de Villemeur, Thierry; Héron, Bénédicte; Dalbies, Florence; Cador, Bérengère; Guemann, Anne-Sophie; Gaches, Francis; Hivert, Bénédicte; Leguy-Seguin, Vanessa; Masseau, Agathe; Deshayes, Robin; Pers, Yves-Marie; Pettazzoni, Magali; Bekri, Soumeya; Caillaud, Catherine; Le Guillou, Edouard; Szymanowski, Marie; Astudillo, Leonardo; Mauhin, Wladimir; Nadjar, Yann; Serratrice, Christine; Berger, Marc G; Camou, Fabrice; Belmatoug, Nadia; Stirnemann, Jérôme

French national diagnosis and care protocol (Protocole National De Diagnostic et de Soins; PNDS): Gaucher disease

法国国家诊断和治疗方案(Protocole National De Diagnostic et de Soins;PNDS):戈谢病

Camou, Fabrice; Serratrice, Christine; Pettazzoni, Magali; Nadjar, Yann; Brassier, Anaïs; Bekri, Soumeya; Cador-Rousseau, Bérengère; Dagneaux, Louis; Dalbies, Florence; Froissart, Roseline; Genevaz, Delphine; Guemann, Anne-Sophie; Hivert, Bénédicte; Leguy-Seguin, Vanessa; Marcel, Catherine; Masseau, Agathe; Michaud, Martin; Pers, Yves-Marie; Stirnemann, Jérôme; Vergnaud, Sabrina; Nguyen, Yann; Caillaud, Catherine; Pichard, Samia; Berger, Marc G; Belmatoug, Nadia

High flow oxygen for vaso-occlusive crisis: a multicentre, prospective, randomised, multi-arm, multi-stage clinical trial (OSONE)

高流量氧疗治疗血管阻塞危象:一项多中心、前瞻性、随机、多组、多阶段临床试验(OSONE)

Mekontso Dessap, Armand; Habibi, Anoosha; Guillaud, Constance; Kassasseya, Christian; Larrat, Charlotte; Agbakou, Maïté; Tchoubou, Tona; Candille, Clara; Carpentier, Benjamin; Landais, Mickael; Arlet, Jean-Benoît; Fartoukh, Muriel; Desclaux, Arnaud; Masseau, Agathe; Oziel, Johanna; Bouharaoua, Sihem; Affo, Comlan; Viglino, Damien; Boukari, Latifatou; Martin, Luis Ensenyat; Ngo, Stéphanie; Anguel, Nadia; Chantalat, Christelle; Bourgarit-Durand, Anne; Genty, Isabelle; Makowski, Caroline; Guillet, Stéphanie; Melica, Giovanna; Lionnet, François; Le Jeune, Sylvain; Joseph, Laure; Lanternier, Fanny; Cougoul, Pierre; Bertchansky, Ivan; Boue, Yvonnick; Bartolucci, Pablo; Gendreau, Ségolène; Audureau, Etienne

Lower esophageal sphincter achalasia-like syndrome causing megaesophagus in a cat

猫的下食管括约肌失弛症样综合征导致巨食管症

Reinero, Carol; Grobman, Megan; Vientós-Plotts, Aida; Masseau, Isabelle; Gerhard, Charlotte

Substance use disorder of equimolar oxygen-nitrous oxide mixture in French sickle-cell patients: results of the PHEDRE study

法国镰状细胞贫血症患者等摩尔氧气-一氧化二氮混合物物质使用障碍:PHEDRE 研究结果

Gérardin, Marie; Rousselet, Morgane; Couec, Marie-Laure; Masseau, Agathe; Aquizerate, Aurélie; Authier, Nicolas; Deheul, Sylvie; Roussin, Anne; Micallef, Joelle; Djezzar, Samira; Feuillet, Fanny; Jolliet, Pascale; Grall-Bronnec, Marie; Victorri-Vigneau, Caroline

Clinical and Prognostic Factors in Patients with IgG4-Related Kidney Disease

IgG4相关肾病患者的临床和预后因素

Chaba, Anis; Devresse, Arnaud; Audard, Vincent; Boffa, Jean Jacques; Karras, Alexandre; Cartery, Claire; Deltombe, Clément; Chemouny, Jonathan; Contamin, Claudine; Courivaud, Cecile; Duquennoy, Simon; Garcia, Hugo; Joly, Dominique; Goumri, Nabila; Hanouna, Guillaume; Halimi, Jean Michel; Plaisier, Emmanuelle; Hamidou, Mohamed; Landron, Cédric; Launay, David; Lebas, Celine; Legendre, Mathieu; Masseau, Agathe; Mathian, Alexis; Mercadal, Lucile; Morel, Nathalie; Mutinelli-Szymanski, Prisca; Palat, Sylvain; Pennaforte, Jean-Loup; Peraldi, Marie Noelle; Pozdzik, Agnieszka; Schleinitz, Nicolas; Thaunat, Olivier; Titeca-Beauport, Dimitri; Mussini, Charlotte; Touati, Sonia; Prinz, Eric; Faller, Anne Laure; Richter, Sarah; Vilaine, Eve; Ferlicot, Sophie; Von-Kotze, Clarissa; Belliere, Julie; Olagne, Jerome; Mesbah, Rafik; Snanoudj, Renaud; Nouvier, Mathilde; Ebbo, Mikael; Zaidan, Mohamad

Sphingosine-1-Phosphate Levels Are Higher in Male Patients with Non-Classic Fabry Disease

非经典法布里病男性患者的鞘氨醇-1-磷酸水平较高

Wladimir Mauhin, Abdellah Tebani, Damien Amelin, Lenaig Abily-Donval, Foudil Lamari, Jonathan London, Claire Douillard, Bertrand Dussol, Vanessa Leguy-Seguin, Esther Noel, Agathe Masseau, Didier Lacombe, Hélène Maillard, Soumeya Bekri, Olivier Lidove, Olivier Benveniste4