Intramuscular Evaluation of Chimeric Locked Nucleic Acid/2'OMethyl-Modified Antisense Oligonucleotides for Targeted Exon 23 Skipping in Mdx Mice
嵌合型锁核酸/2'-甲基修饰反义寡核苷酸靶向外显子23跳跃在Mdx小鼠中的肌内注射评价
期刊:Pharmaceuticals
影响因子:4.8
doi:10.3390/ph14111113
Georgiadou, Michaella; Christou, Melina; Sokratous, Kleitos; Wengel, Jesper; Michailidou, Kyriaki; Kyriacou, Kyriacos; Koutsoulidou, Andrie; Mastroyiannopoulos, Nikolaos P; Phylactou, Leonidas A