Vorinostat Improves Myotonic Dystrophy Type 1 Splicing Abnormalities in DM1 Muscle Cell Lines and Skeletal Muscle from a DM1 Mouse Model
伏立诺他可改善 DM1 小鼠模型中 DM1 肌肉细胞系和骨骼肌中的 1 型强直性肌营养不良症剪接异常
期刊:International Journal of Molecular Sciences
影响因子:0.7
doi:10.3390/ijms24043794
Nafisa Neault, Aymeric Ravel-Chapuis, Stephen D Baird, John A Lunde, Mathieu Poirier, Emiliyan Staykov, Julio Plaza-Diaz, Gerardo Medina, Francisco Abadía-Molina, Bernard J Jasmin, Alex E MacKenzie