日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Systematic pegRNA design with PRIDICT2.0 and ePRIDICT for efficient prime editing

利用PRIDICT2.0和ePRIDICT进行系统性的pegRNA设计,以实现高效的先导编辑

Mathis, Nicolas; Marquart, Kim Fabiano; Allam, Ahmed; Krauthammer, Michael; Schwank, Gerald

Spatial profiling of gene editing by in situ sequencing in mice and macaques

利用原位测序技术对小鼠和猕猴的基因编辑进行空间分析

Janjuha, Sharan; Haenggi, Tatjana; Chamberlain, Thomas C; Rothgangl, Tanja; Kissling, Lucas; Wilhelm, Maria; Mathis, Nicolas; Boeck, Desiree; Marquart, Kim; Ioannidi, Eleonora; Moon, Woohyun J; Muramatsu, Hiromi; Vadovics, Máté; Pardi, Norbert; Semple, Sean C; Tam, Ying K; Schwank, Gerald

LDLR variant classification through activity-normalized prime editing screening

通过活性归一化先导编辑筛选进行LDLR变异分类

Zhou, Phillip J; Velimirovic, Minja; Yu, Tian; Gligorovski, Vojislav; Mathis, Nicolas; Zhao, Jing; Phan, Quang Vinh; Vogd, Felicitas; Ryu, Jayoung; Pan, Qisheng; Tyagi, Atharva; Ascher, David B; Schwank, Gerald; Pinello, Luca; Cassa, Christopher A; Sherwood, Richard I

Machine learning prediction of prime editing efficiency across diverse chromatin contexts

利用机器学习预测不同染色质环境下的酶促编辑效率

Mathis, Nicolas; Allam, Ahmed; Tálas, András; Kissling, Lucas; Benvenuto, Elena; Schmidheini, Lukas; Schep, Ruben; Damodharan, Tanav; Balázs, Zsolt; Janjuha, Sharan; Ioannidi, Eleonora I; Böck, Desirée; van Steensel, Bas; Krauthammer, Michael; Schwank, Gerald

Effective genome editing with an enhanced ISDra2 TnpB system and deep learning-predicted ωRNAs.

利用增强型 ISDra2 TnpB 系统和深度学习预测的 αRNA 进行有效的基因组编辑

Marquart Kim Fabiano, Mathis Nicolas, Mollaysa Amina, Müller Saphira, Kissling Lucas, Rothgangl Tanja, Schmidheini Lukas, Kulcsár Péter István, Allam Ahmed, Kaufmann Masako M, Matsushita Mai, Haenggi Tatjana, Cathomen Toni, Kopf Manfred, Krauthammer Michael, Schwank Gerald

Replacing the SpCas9 HNH domain by deaminases generates compact base editors with an alternative targeting scope

用脱氨酶替换 SpCas9 的 HNH 结构域可生成具有不同靶向范围的紧凑型碱基编辑器

Villiger, Lukas; Schmidheini, Lukas; Mathis, Nicolas; Rothgangl, Tanja; Marquart, Kim; Schwank, Gerald

Characterization of two novel intronic OPA1 mutations resulting in aberrant pre-mRNA splicing

对两种导致异常前体mRNA剪接的新型OPA1内含子突变进行表征

Bolognini, Ramona; Gerth-Kahlert, Christina; Abegg, Mathias; Bartholdi, Deborah; Mathis, Nicolas; Sturm, Veit; Gallati, Sabina; Schaller, André