Widespread Gene Editing in the Brain via In Utero Delivery of mRNA Using Acid-Degradable Lipid Nanoparticles
利用酸可降解脂质纳米粒子在子宫内递送 mRNA,实现大脑的广泛基因编辑
期刊:ACS Nano
影响因子:15.8
doi:10.1021/acsnano.4c05169
Kewa Gao, Hesong Han, Matileen G Cranick, Sheng Zhao, Shanxiu Xu, Boyan Yin, Hengyue Song, Yibo Hu, Maria T Clarke, David Wang, Jessica M Wong, Zehua Zhao, Benjamin W Burgstone, Diana L Farmer, Niren Murthy, Aijun Wang