Gene correction for SCID-X1 in long-term hematopoietic stem cells
长期造血干细胞中 SCID-X1 的基因校正
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-019-09614-y
Mara Pavel-Dinu, Volker Wiebking, Beruh T Dejene, Waracharee Srifa, Sruthi Mantri, Carmencita E Nicolas, Ciaran Lee, Gang Bao, Eric J Kildebeck, Niraj Punjya, Camille Sindhu, Matthew A Inlay, Nivedita Saxena, Suk See DeRavin, Harry Malech, Maria Grazia Roncarolo, Kenneth I Weinberg, Matthew H Porteu