日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

PRMT inhibitor promotes SMN2 exon 7 inclusion and synergizes with nusinersen to rescue SMA mice

PRMT 抑制剂促进 SMN2 外显子 7 插入并与 nusinersen 协同作用挽救 SMA 小鼠

Anna J Kordala, Jessica Stoodley, Nina Ahlskog, Muhammad Hanifi, Antonio Garcia Guerra, Amarjit Bhomra, Wooi Fang Lim, Lyndsay M Murray, Kevin Talbot, Suzan M Hammond, Matthew Ja Wood, Carlo Rinaldi

Antibody-oligonucleotide conjugate achieves CNS delivery in animal models for spinal muscular atrophy

抗体-寡核苷酸偶联物在脊髓性肌萎缩动物模型中实现了中枢神经系统递送

Suzan M Hammond, Frank Abendroth, Larissa Goli, Jessica Stoodley, Matthew Burrell, George Thom, Ian Gurrell, Nina Ahlskog, Michael J Gait, Matthew Ja Wood, Carl I Webster

Combining multiomics and drug perturbation profiles to identify muscle-specific treatments for spinal muscular atrophy

结合多组学和药物扰动谱来确定脊髓性肌萎缩症的肌肉特异性治疗方法

Katharina E Meijboom, Viola Volpato, Jimena Monzón-Sandoval, Joseph M Hoolachan, Suzan M Hammond, Frank Abendroth, Olivier G de Jong, Gareth Hazell, Nina Ahlskog, Matthew Ja Wood, Caleb Webber, Melissa Bowerman

Profiling of Extracellular Small RNAs Highlights a Strong Bias towards Non-Vesicular Secretion

细胞外小RNA的分析突出了对非囊泡分泌的强烈偏好

Helena Sork, Mariana Conceicao, Giulia Corso, Joel Nordin, Yi Xin Fiona Lee, Kaarel Krjutskov, Jakub Orzechowski Westholm, Pieter Vader, Marie Pauwels, Roosmarijn E Vandenbroucke, Matthew Ja Wood, Samir El Andaloussi, Imre Mäger

Are telephone consultations the future of the NHS? The outcomes and experiences of an NHS urological service in moving to telemedicine

电话问诊会是英国国民医疗服务体系(NHS)的未来吗?NHS泌尿科服务向远程医疗转型后的成果和经验

Efthymiadis, Agathoklis; Hart, Edward Jm; Guy, Alexandra M; Harry, Rebecca; Mahesan, Tharani; Chedid, Wissam Abou; Uribe-Lewis, Santiago; Perry, Matthew Ja

Exosomes mediate sensory hair cell protection in the inner ear

外泌体介导内耳感觉毛细胞保护

Andrew M Breglio, Lindsey A May, Melanie Barzik, Nora C Welsh, Shimon P Francis, Tucker Q Costain, Lizhen Wang, D Eric Anderson, Ronald S Petralia, Ya-Xian Wang, Thomas B Friedman, Matthew Ja Wood, Lisa L Cunningham

Peptide-conjugated oligonucleotides evoke long-lasting myotonic dystrophy correction in patient-derived cells and mice

肽偶联寡核苷酸可在患者来源细胞和小鼠中诱导持久的肌强直性营养不良症矫正

Klein, Arnaud F; Varela, Miguel A; Arandel, Ludovic; Holland, Ashling; Naouar, Naira; Arzumanov, Andrey; Seoane, David; Revillod, Lucile; Bassez, Guillaume; Ferry, Arnaud; Jauvin, Dominic; Gourdon, Genevieve; Puymirat, Jack; Gait, Michael J; Furling, Denis; Wood, Matthew Ja

Lipid-based Transfection Reagents Exhibit Cryo-induced Increase in Transfection Efficiency

基于脂质的转染试剂表现出低温诱导的转染效率提高

Helena Sork, Joel Z Nordin, Janne J Turunen, Oscar Pb Wiklander, Burcu Bestas, Eman M Zaghloul, Helerin Margus, Kärt Padari, Adil D Duru, Giulia Corso, Jeremy Bost, Pieter Vader, Margus Pooga, Ci Edvard Smith, Matthew Ja Wood, Raymond M Schiffelers, Mattias Hällbrink, Samir El Andaloussi

Dual Myostatin and Dystrophin Exon Skipping by Morpholino Nucleic Acid Oligomers Conjugated to a Cell-penetrating Peptide Is a Promising Therapeutic Strategy for the Treatment of Duchenne Muscular Dystrophy

通过与细胞穿透肽结合的吗啉核酸寡聚体进行双重肌生长抑制素和肌营养不良蛋白外显子跳跃是治疗杜氏肌营养不良症的一种有前途的治疗策略

Alberto Malerba, Jagjeet K Kang, Graham McClorey, Amer F Saleh, Linda Popplewell, Michael J Gait, Matthew Ja Wood, George Dickson

Small RNA-Mediated Epigenetic Myostatin Silencing

小RNA介导的表观遗传肌生长抑制素沉默

Thomas C Roberts, Samir El Andaloussi, Kevin V Morris, Graham McClorey, Matthew Ja Wood