日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Inducible Expression of GDNF in Transplanted iPSC-Derived Neural Progenitor Cells

移植的iPSC衍生神经祖细胞中GDNF的诱导表达

Akhtar, Aslam Abbasi; Gowing, Genevieve; Kobritz, Naomi; Savinoff, Steve E; Garcia, Leslie; Saxon, David; Cho, Noell; Kim, Gibum; Tom, Colton M; Park, Hannah; Lawless, George; Shelley, Brandon C; Mattis, Virginia B; Breunig, Joshua J; Svendsen, Clive N

Analysis of a read-through promoting compound in a severe mouse model of spinal muscular atrophy

在严重脊髓性肌萎缩症小鼠模型中对一种促进通读的化合物进行分析

Mattis, Virginia B; Tom Chang, Cheng-Wei; Lorson, Christian L

Delivery of recombinant follistatin lessens disease severity in a mouse model of spinal muscular atrophy

在脊髓性肌萎缩症小鼠模型中,重组卵泡抑素的递送可减轻疾病严重程度。

Rose, Ferrill F Jr; Mattis, Virginia B; Rindt, Hansjörg; Lorson, Christian L

Delivery of a read-through inducing compound, TC007, lessens the severity of a spinal muscular atrophy animal model

递送一种通读诱导化合物TC007可减轻脊髓性肌萎缩症动物模型的严重程度。

Mattis, Virginia B; Ebert, Allison D; Fosso, Marina Y; Chang, Cheng-Wei; Lorson, Christian L

Subcutaneous administration of TC007 reduces disease severity in an animal model of SMA

皮下注射TC007可减轻SMA动物模型中的疾病严重程度。

Mattis, Virginia B; Fosso, Marina Y; Chang, Cheng-Wei; Lorson, Christian L

Detection of human survival motor neuron (SMN) protein in mice containing the SMN2 transgene: applicability to preclinical therapy development for spinal muscular atrophy.

在含有 SMN2 转基因的小鼠中检测人类存活运动神经元 (SMN) 蛋白:对脊髓性肌萎缩症临床前治疗开发的适用性

Mattis Virginia B, Butchbach Matthew E R, Lorson Christian L

A SMNDelta7 read-through product confers functionality to the SMNDelta7 protein

SMNDelta7 通读产物赋予 SMNDelta7 蛋白功能。

Mattis, Virginia B; Bowerman, Melissa; Kothary, Rashmi; Lorson, Christian L