Systemic delivery of siRNA down regulates brain prion protein and ameliorates neuropathology in prion disorder
全身性递送siRNA可下调脑内朊病毒蛋白,并改善朊病毒疾病的神经病理学症状。
期刊:PLoS One
影响因子:2.6
doi:10.1371/journal.pone.0088797
Lehmann, Sylvain; Relano-Gines, Aroa; Resina, Sarah; Brillaud, Elsa; Casanova, Danielle; Vincent, Charles; Hamela, Claire; Poupeau, Sophie; Laffont, Mathieu; Gabelle, Audrey; Delaby, Constance; Belondrade, Maxime; Arnaud, Jacques-Damien; Alvarez, Maria-Teresa; Maurel, Jean-Claude; Maurel, Patrick; Crozet, Carole