Corrective GUSB transfer to the canine mucopolysaccharidosis VII brain
将矫正性GUSB移植到犬粘多糖贮积症VII型脑组织中
期刊:Molecular Therapy
影响因子:12
doi:10.1038/mt.2013.283
Cubizolle, Aurelie; Serratrice, Nicolas; Skander, Nadia; Colle, Marie-Anne; Ibanes, Sandy; Gennetier, Aurelie; Bayo-Puxan, Neus; Mazouni, Khalil; Mennechet, Franck; Joussemet, Beatrice; Cherel, Yan; Lajat, Yaouen; Vite, Charles; Bernex, Florence; Kalatzis, Vasiliki; Haskins, Mark E; Kremer, Eric J