日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

Evaluating the state of the science for adeno-associated virus integration: An integrated perspective

评估腺相关病毒整合的科学现状：一个综合视角

期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2022.06.004
Sabatino, Denise E; Bushman, Frederic D; Chandler, Randy J; Crystal, Ronald G; Davidson, Beverly L; Dolmetsch, Ricardo; Eggan, Kevin C; Gao, Guangping; Gil-Farina, Irene; Kay, Mark A; McCarty, Douglas M; Montini, Eugenio; Ndu, Adora; Yuan, Jing
微生物学
发表日期：2022
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Topics in AAV integration come front and center at ASGCT AAV Integration Roundtable

ASGCT AAV 集成圆桌会议将 AAV 集成相关议题置于中心位置。

期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2021.10.024
Sabatino, Denise E; McCarty, Douglas M
发表日期：2021
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Targeting Root Cause by Systemic scAAV9-hIDS Gene Delivery: Functional Correction and Reversal of Severe MPS II in Mice

通过系统性scAAV9-hIDS基因递送靶向病因：小鼠严重MPS II的功能矫正和逆转

期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2018.07.005
Fu, Haiyan; Zaraspe, Kim; Murakami, Naoko; Meadows, Aaron S; Pineda, Ricardo J; McCarty, Douglas M; Muenzer, Joseph
发表日期：2018
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Differential Prevalence of Antibodies Against Adeno-Associated Virus in Healthy Children and Patients with Mucopolysaccharidosis III: Perspective for AAV-Mediated Gene Therapy

健康儿童和粘多糖贮积症III型患者体内抗腺相关病毒抗体的差异流行率：AAV介导的基因治疗展望

期刊:Human Gene Therapy Clinical Development
影响因子:
doi:10.1089/humc.2017.109
Fu, Haiyan; Meadows, Aaron S; Pineda, Ricardo J; Kunkler, Krista L; Truxal, Kristen V; McBride, Kim L; Flanigan, Kevin M; McCarty, Douglas M
基因治疗
微生物学
发表日期：2017
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Functional correction of neurological and somatic disorders at later stages of disease in MPS IIIA mice by systemic scAAV9-hSGSH gene delivery

通过全身性scAAV9-hSGSH基因递送，在MPS IIIA小鼠疾病后期实现神经系统和躯体疾病的功能性矫正。

期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1038/mtm.2016.36
Fu, Haiyan; Cataldi, Marcela P; Ware, Tierra A; Zaraspe, Kimberly; Meadows, Aaron S; Murrey, Darren A; McCarty, Douglas M
发表日期：2016
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Blood genome-wide transcriptional profiles reflect broad molecular impairments and strong blood-brain links in Alzheimer's disease

血液全基因组转录谱反映了阿尔茨海默病中广泛的分子损伤和强烈的血脑联系

期刊:Journal of Alzheimers Disease
影响因子:3.1
doi:10.3233/JAD-140606
Naughton, Bartholomew J; Duncan, F Jason; Murrey, Darren A; Meadows, Aaron S; Newsom, David E; Stoicea, Nicoleta; White, Peter; Scharre, Douglas W; Mccarty, Douglas M; Fu, Haiyan
阿尔茨海默症
神经科学
发表日期：2015
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Feasibility and safety of systemic rAAV9-hNAGLU delivery for treating mucopolysaccharidosis IIIB: toxicology, biodistribution, and immunological assessments in primates

全身性rAAV9-hNAGLU递送治疗粘多糖贮积症IIIB的可行性和安全性：灵长类动物毒理学、生物分布和免疫学评估

期刊:Human Gene Therapy Clinical Development
影响因子:
doi:10.1089/humc.2013.208
Murrey, Darren A; Naughton, Bartholomew J; Duncan, F Jason; Meadows, Aaron S; Ware, Tierra A; Campbell, Katie J; Bremer, William G; Walker, Christopher M; Goodchild, Laurie; Bolon, Brad; La Perle, Krista; Flanigan, Kevin M; McBride, Kim L; McCarty, Douglas M; Fu, Haiyan
免疫/内分泌
发表日期：2014
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Peripheral nervous system neuropathology and progressive sensory impairments in a mouse model of Mucopolysaccharidosis IIIB

粘多糖贮积症 IIIB 型小鼠模型的周围神经系统病理学改变和进行性感觉障碍

期刊:PLoS One
影响因子:
doi:10.1371/journal.pone.0045992
Fu, Haiyan; Bartz, Julianne D; Stephens, Robert L Jr; McCarty, Douglas M
发表日期：2012
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Mucopolysaccharidosis IIIB, a lysosomal storage disease, triggers a pathogenic CNS autoimmune response

黏多糖贮积症IIIB型是一种溶酶体贮积症，可引发致病性中枢神经系统自身免疫反应。

期刊:Journal of Neuroinflammation
影响因子:10.1
doi:10.1186/1742-2094-7-39
Killedar, Smruti; Dirosario, Julianne; Divers, Erin; Popovich, Phillip G; McCarty, Douglas M; Fu, Haiyan
神经科学
免疫/内分泌
发表日期：2010
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Host cell DNA repair pathways in adeno-associated viral genome processing.

腺相关病毒基因组加工中的宿主细胞DNA修复途径

期刊:Journal of Virology
影响因子:3.8
doi:10.1128/JVI.00841-06
Choi Vivian W, McCarty Douglas M, Samulski R Jude
细胞生物学
Viral
发表日期：2006
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