Efficacy and ototoxicity of different cyclodextrins in Niemann-Pick C disease
不同环糊精对尼曼-匹克C病的疗效及耳毒性
期刊:Annals of Clinical and Translational Neurology
影响因子:4.4
doi:10.1002/acn3.306
Cristin D Davidson, Yonatan I Fishman, István Puskás, Julianna Szemán, Tamás Sohajda, Leslie A McCauliff, Jakub Sikora, Judith Storch, Marie T Vanier, Lajos Szente, Steven U Walkley, Kostantin Dobrenis