日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

Comparison of CRISPR-Cas13b RNA base editing approaches for USH2A-associated inherited retinal degeneration

比较 CRISPR-Cas13b RNA 碱基编辑方法在 USH2A 相关遗传性视网膜变性中的应用

期刊:Communications Biology
影响因子:5.1
doi:10.1038/s42003-025-07557-3
Fry, Lewis E; Major, Lauren; Salman, Ahmed; McDermott, Lucy A; Yang, Jun; King, Andrew J; McClements, Michelle E; MacLaren, Robert E
碱基编辑
发表日期：2025
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Gene Therapy Strategies for the Treatment of Bestrophinopathies

治疗贝斯特罗芬病基因治疗策略

期刊:International Journal of Molecular Sciences
影响因子:4.9
doi:10.3390/ijms26199421
Haldrup, Silja B; McClements, Michelle E; Cehajic-Kapetanovic, Jasmina; Corydon, Thomas J; MacLaren, Robert E
基因治疗
发表日期：2025
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CRISPR targeting of SNPs associated with age-related macular degeneration in ARPE-19 cells: a potential model for manipulating the complement system.

利用 CRISPR 技术靶向 ARPE-19 细胞中与年龄相关性黄斑变性相关的 SNP：一种操纵补体系统的潜在模型

期刊:Gene Therapy
影响因子:4.5
doi:10.1038/s41434-025-00522-z
Salman Ahmed, Song Won Kyung, Storm Tina, McClements Michelle E, MacLaren Robert E
细胞生物学
发表日期：2025
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CRISPR Manipulation of Age-Related Macular Degeneration Haplotypes in the Complement System: Potential Future Therapeutic Applications/Avenues

利用 CRISPR 技术操控补体系统中与年龄相关性黄斑变性相关的单倍型：潜在的未来治疗应用/途径

期刊:International Journal of Molecular Sciences
影响因子:4.9
doi:10.3390/ijms25031697
Salman, Ahmed; McClements, Michelle E; MacLaren, Robert E
免疫/内分泌
发表日期：2024
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Gene Therapies in Clinical Development to Treat Retinal Disorders

处于临床开发阶段的基因疗法用于治疗视网膜疾病

期刊:Molecular Diagnosis & Therapy
影响因子:4.4
doi:10.1007/s40291-024-00722-0
McClements, Michelle E; Elsayed, Maram E A Abdalla; Major, Lauren; de la Camara, Cristina Martinez-Fernandez; MacLaren, Robert E
发表日期：2024
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Single-cell transcriptomic analysis of retinal immune regulation and blood-retinal barrier function during experimental autoimmune uveitis

实验性自身免疫性葡萄膜炎期间视网膜免疫调节和血视网膜屏障功能的单细胞转录组分析

期刊:Scientific Reports
影响因子:3.9
doi:10.1038/s41598-024-68401-y
Quinn, Joel; Salman, Ahmed; Paluch, Christopher; Jackson-Wood, Matthew; McClements, Michelle E; Luo, Jian; Davis, Simon J; Cornall, Richard J; MacLaren, Robert E; Dendrou, Calliope A; Xue, Kanmin
细胞生物学
单细胞
免疫/内分泌
发表日期：2024
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Future Perspectives of Prime Editing for the Treatment of Inherited Retinal Diseases

基因编辑在治疗遗传性视网膜疾病中的未来展望

期刊:Cells
影响因子:5.2
doi:10.3390/cells12030440
Hansen, Silja; McClements, Michelle E; Corydon, Thomas J; MacLaren, Robert E
发表日期：2023
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A Review of CRISPR Tools for Treating Usher Syndrome: Applicability, Safety, Efficiency, and In Vivo Delivery

CRISPR工具在治疗Usher综合征中的应用综述：适用性、安全性、有效性和体内递送

期刊:International Journal of Molecular Sciences
影响因子:4.9
doi:10.3390/ijms24087603
Major, Lauren; McClements, Michelle E; MacLaren, Robert E
发表日期：2023
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Erratum: Enhancement of Adeno-Associated Virus-Mediated Gene Therapy Using Hydroxychloroquine in Murine and Human Tissues

勘误：羟氯喹增强腺相关病毒介导的基因治疗在小鼠和人体组织中的疗效

期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2023.01.001
Chandler, Laurel C; Barnard, Alun R; Caddy, Sarah L; Patrício, Maria I; McClements, Michelle E; Fu, Howell; Rada, Cristina; MacLaren, Robert E; Xue, Kanmin
微生物学
Human
基因治疗
发表日期：2023
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Programmable RNA editing with endogenous ADAR enzymes - a feasible option for the treatment of inherited retinal disease?

利用内源性ADAR酶进行可编程RNA编辑——治疗遗传性视网膜疾病的可行方案？

期刊:Frontiers in Molecular Neuroscience
影响因子:3.8
doi:10.3389/fnmol.2023.1092913
Bellingrath, Julia-Sophia; McClements, Michelle E; Fischer, M Dominik; MacLaren, Robert E
ADA
发表日期：2023
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