日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Systematic optimization of prime editing for the efficient functional correction of CFTR F508del in human airway epithelial cells

系统优化主编辑策略,以实现人呼吸道上皮细胞中CFTR F508del突变的有效功能性矫正

Sousa, Alexander A; Hemez, Colin; Lei, Lei; Traore, Soumba; Kulhankova, Katarina; Newby, Gregory A; Doman, Jordan L; Oye, Keyede; Pandey, Smriti; Karp, Philip H; McCray, Paul B Jr; Liu, David R

IL-13 decreases susceptibility to airway epithelial SARS-CoV-2 infection but increases disease severity in vivo via eicosanoid signalling

IL-13通过类花生酸信号通路降低气道上皮细胞对SARS-CoV-2感染的易感性,但增加体内疾病的严重程度。

Ghimire, Shreya; Xue, Biyun; Li, Kun; Gannon, Ryan M; Wohlford-Lenane, Christine L; Thurman, Andrew L; Gong, Huiyu; Necker, Grace C; Zheng, Jian; Meyerholz, David K; Perlman, Stanley; McCray, Paul B Jr; Pezzulo, Alejandro A

CF airway epithelia display exaggerated host defense responses and prolonged cilia loss during RSV infection

囊性纤维化气道上皮在呼吸道合胞病毒感染期间表现出过度的宿主防御反应和纤毛脱落延长。

Bartlett, Jennifer A; Huntemann, Eric D; Krishnamurthy, Sateesh; Hartwig, Stacey M; Pewa, Alvin; Thurman, Andrew L; Chimenti, Michael S; Taylor, Eric B; Varga, Steven M; McCray, Paul B Jr

Do pulmonary ionocytes absorb chloride or secrete chloride?

肺泡离子细胞是吸收氯离子还是分泌氯离子?

Thornell, Ian M; Lei, Lei; McCray, Paul B Jr; Welsh, Michael J

Lentiviral-mediated gene complementation rescues pathogenic ABCA3 variants

慢病毒介导的基因互补可挽救致病性ABCA3变体

Cooney, Ashley L; Lamer, Shakayla; Yang, Ping; Wegner, Daniel J; White, Frances V; Cole, F Sessions; Wohlford-Lenane, Chris; Hennessey, Erin; Bawa, Pushpinder; Kotton, Darrell N; Sinn, Patrick L; Wambach, Jennifer A; McCray, Paul B Jr

Amphiphilic shuttle peptide delivers base editor ribonucleoprotein to correct the CFTR R553X mutation in well-differentiated airway epithelial cells.

两亲性穿梭肽将碱基编辑器核糖核蛋白递送至分化良好的气道上皮细胞,以纠正 CFTR R553X 突变

Kulhankova Katarina, Cheng Anna X, Traore Soumba, Auger Maud, Pelletier Mia, Hervault Maxime, Wells Kevin D, Green Jonathan A, Byrne Addison, Nelson Benjamin, Sponchiado Mariana, Boosani Chandra, Heffner Caleb S, Snow Kathy J, Murray Stephen A, Villacreses Raul A, Rector Michael V, Gansemer Nicholas D, Stoltz David A, Allamargot Chantal, Couture Frédéric, Hemez Colin, Hallée Stéphanie, Barbeau Xavier, Harvey Mario, Lauvaux Coraline, Gaillet Bruno, Newby Gregory A, Liu David R, McCray Paul B Jr, Guay David

Dynamic measurement of airway surface liquid volume with an ex vivo trachea-chip

利用离体气管芯片动态测量气道表面液体体积

Scott, Michael; Lei, Lei; Bierstedt, Kaleb C; McCray, Paul B Jr; Xie, Yuliang

Development and Initial Characterization of Pigs with DNAI1 Mutations and Primary Ciliary Dyskinesia

DNAI1突变和原发性纤毛运动障碍猪的发育和初步表征

Abou Alaiwa, Mahmoud A; Hilkin, Brie M; Price, Margaret P; Gansemer, Nicholas D; Rector, Michael R; Stroik, Mal R; Powers, Linda S; Whitworth, Kristin M; Samuel, Melissa S; Jain, Akansha; Ostedgaard, Lynda S; Ernst, Sarah E; Philibert, Winter; Boyken, Linda D; Moninger, Thomas O; Karp, Phillip H; Hornick, Douglas B; Sinn, Patrick L; Fischer, Anthony J; Pezzulo, Alejandro A; McCray, Paul B Jr; Meyerholz, David K; Zabner, Joseph; Prather, Randy S; Welsh, Michael J; Stoltz, David A

The NIH Somatic Cell Genome Editing program

美国国立卫生研究院体细胞基因组编辑计划

Saha, Krishanu; Sontheimer, Erik J; Brooks, P J; Dwinell, Melinda R; Gersbach, Charles A; Liu, David R; Murray, Stephen A; Tsai, Shengdar Q; Wilson, Ross C; Anderson, Daniel G; Asokan, Aravind; Banfield, Jillian F; Bankiewicz, Krystof S; Bao, Gang; Bulte, Jeff W M; Bursac, Nenad; Campbell, Jarryd M; Carlson, Daniel F; Chaikof, Elliot L; Chen, Zheng-Yi; Cheng, R Holland; Clark, Karl J; Curiel, David T; Dahlman, James E; Deverman, Benjamin E; Dickinson, Mary E; Doudna, Jennifer A; Ekker, Stephen C; Emborg, Marina E; Feng, Guoping; Freedman, Benjamin S; Gamm, David M; Gao, Guangping; Ghiran, Ionita C; Glazer, Peter M; Gong, Shaoqin; Heaney, Jason D; Hennebold, Jon D; Hinson, John T; Khvorova, Anastasia; Kiani, Samira; Lagor, William R; Lam, Kit S; Leong, Kam W; Levine, Jon E; Lewis, Jennifer A; Lutz, Cathleen M; Ly, Danith H; Maragh, Samantha; McCray, Paul B Jr; McDevitt, Todd C; Mirochnitchenko, Oleg; Morizane, Ryuji; Murthy, Niren; Prather, Randall S; Ronald, John A; Roy, Subhojit; Roy, Sushmita; Sabbisetti, Venkata; Saltzman, W Mark; Santangelo, Philip J; Segal, David J; Shimoyama, Mary; Skala, Melissa C; Tarantal, Alice F; Tilton, John C; Truskey, George A; Vandsburger, Moriel; Watts, Jonathan K; Wells, Kevin D; Wolfe, Scot A; Xu, Qiaobing; Xue, Wen; Yi, Guohua; Zhou, Jiangbing

The first few days of a SARS-CoV-2 infection viewed at single-cell resolution

以单细胞分辨率观察SARS-CoV-2感染最初几天的过程

Gallagher, Tom; McCray, Paul B Jr