Regulatory strategies for rare diseases under current global regulatory statutes: a discussion with stakeholders
当前全球监管法规下罕见病监管策略:与利益相关者的讨论
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-019-1017-5
Mulberg, Andrew E; Bucci-Rechtweg, Christina; Giuliano, Joseph; Jacoby, David; Johnson, Franklin K; Liu, Qing; Marsden, Deborah; McGoohan, Scott; Nelson, Robert; Patel, Nita; Romero, Klaus; Sinha, Vikram; Sitaraman, Sheela; Spaltro, John; Kessler, Vivian