日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Cardiac safety of fordadistrogene movaparvovec gene therapy in Duchenne muscular dystrophy: Initial observations from a phase 1b trial

杜氏肌营养不良症患者接受 fordadistrogene movaparvovec 基因治疗的心脏安全性:一项 1b 期试验的初步观察结果

Sherlock, Sarah P; Levy, Daniel I; McIntosh, Avery; Shieh, Perry B; Smith, Edward C; McDonnell, Tara G; Ryan, Kelly A; Delnomdedieu, Marielle; Binks, Michael; Lal, Ashwin K; Butterfield, Russell J

Evaluation of Mitochondrial Complex 1 Density with [(18)F]BCPP-EF in a Murine Model and Individuals with Friedreich Ataxia.

利用 [(18)F]BCPP-EF 对小鼠模型和弗里德赖希共济失调患者进行线粒体复合物 1 密度评估

Chen Laigao, Rizzo Gaia, Bulawa Christine, Van Dijk Koene R A, Henning Erica C, Martelli Alain, Palmer Jeffrey, McIntosh Avery, Pregel Marko, Sun Pengling, Adewunmi Emmanuel, Aldridge Mark, Chan Jackson, Gunn Roger N, Huiban Mickael, Listanco Allan, Loudon Peter T, Moz Sara, Passchier Jan, Sauvage Lauren, Stewart Rachel, Wells Lisa, Rabiner Eugenii A, Charnas Lawrence R, Festenstein Richard J

Dystrophin/mini-dystrophin expression analysis by immunoaffinity liquid chromatography-tandem mass spectrometry after gene therapy for DMD

采用免疫亲和液相色谱-串联质谱法分析DMD基因治疗后肌营养不良蛋白/迷你肌营养不良蛋白的表达。

Walsh, Jason; Palandra, Joe; Duriga, Nicole; Beidler, David; McIntosh, Avery; Binks, Michael; Neubert, Hendrik

Cell and Gene Therapy: Transforming Treatment Paradigms for Patient-Centric Care

细胞和基因疗法:变革以患者为中心的治疗模式

Yi, Sojeong; Wu, Chia-Yung; McIntosh, Avery; Santaella, Maria E; Robinson, Tara M; Liao, Michael Z

Topical Ocular TRPV1 Antagonist SAF312 (Libvatrep) for Postoperative Pain After Photorefractive Keratectomy

局部眼用TRPV1拮抗剂SAF312(利伐特雷普)用于准分子激光角膜屈光手术后疼痛

Thompson, Vance; Moshirfar, Majid; Clinch, Thomas; Scoper, Stephen; Linn, Steven H; McIntosh, Avery; Li, Yifang; Eaton, Matt; Ferriere, Michael; Stasi, Kalliopi

Navigating the Light-Sheet Image Analysis Software Landscape: Concepts for Driving Cohesion From Data Acquisition to Analysis

探索光片图像分析软件领域:从数据采集到分析的协同发展理念

Gibbs, Holly C; Mota, Sakina M; Hart, Nathan A; Min, Sun Won; Vernino, Alex O; Pritchard, Anna L; Sen, Anindito; Vitha, Stan; Sarasamma, Sreeja; McIntosh, Avery L; Yeh, Alvin T; Lekven, Arne C; McCreedy, Dylan A; Maitland, Kristen C; Perez, Lisa M

Digital endpoints for self-administered home-based functional assessment in pediatric Friedreich's ataxia

儿童弗里德赖希共济失调患者居家自评功能评估的数字化终点

Mueller, Arne; Paterson, Elaine; McIntosh, Avery; Praestgaard, Jens; Bylo, Mary; Hoefling, Holger; Wells, McKenzie; Lynch, David R; Rummey, Christian; Krishnan, Michelle L; Schultz, Meredith; Malanga, C J

Partitioning the risk of tuberculosis transmission in household contact studies

在家庭接触研究中划分结核病传播风险

McIntosh, Avery I; Jenkins, Helen E; Horsburgh, C Robert; Jones-López, Edward C; Whalen, Christopher C; Gaeddert, Mary; Marques-Rodrigues, Patricia; Ellner, Jerrold J; Dietze, Reynaldo; White, Laura F

Incident Mycobacterium tuberculosis infection in household contacts of infectious tuberculosis patients in Brazil

巴西传染性结核病患者家庭接触者中结核分枝杆菌感染病例

Jones-López, Edward C; Acuña-Villaorduña, Carlos; Fregona, Geisa; Marques-Rodrigues, Patricia; White, Laura F; Hadad, David Jamil; Dutra-Molina, Lucilia Pereira; Vinhas, Solange; McIntosh, Avery I; Gaeddert, Mary; Ribeiro-Rodrigues, Rodrigo; Salgame, Padmini; Palaci, Moises; Alland, David; Ellner, Jerrold J; Dietze, Reynaldo

Extensions to Bayesian generalized linear mixed effects models for household tuberculosis transmission

贝叶斯广义线性混合效应模型在家庭结核病传播中的扩展

McIntosh, Avery I; Doros, Gheorghe; Jones-López, Edward C; Gaeddert, Mary; Jenkins, Helen E; Marques-Rodrigues, Patricia; Ellner, Jerrold J; Dietze, Reynaldo; White, Laura F