DNAJB6 isoform specific knockdown: Therapeutic potential for limb girdle muscular dystrophy D1
DNAJB6 亚型特异性敲低:肢带型肌营养不良症 D1 的治疗潜力
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.5
doi:10.1016/j.omtn.2023.05.017
Andrew R Findlay, May M Paing, Jil A Daw, Meade Haller, Rocio Bengoechea, Sara K Pittman, Shan Li, Feng Wang, Timothy M Miller, Heather L True, Tsui-Fen Chou, Conrad C Weihl