Targeting RNA foci in iPSC-derived motor neurons from ALS patients with a C9ORF72 repeat expansion
靶向具有 C9ORF72 重复扩增的 ALS 患者 iPSC 衍生运动神经元中的 RNA 焦点
期刊:Science Translational Medicine
影响因子:15.8
doi:10.1126/scitranslmed.3007529
Dhruv Sareen, Jacqueline G O'Rourke, Pratap Meera, A K M G Muhammad, Sharday Grant, Megan Simpkinson, Shaughn Bell, Sharon Carmona, Loren Ornelas, Anais Sahabian, Tania Gendron, Leonard Petrucelli, Michael Baughn, John Ravits, Matthew B Harms, Frank Rigo, C Frank Bennett, Thomas S Otis, Clive N Sven