Treatment Strategy With Gene Editing for Late-Onset Retinal Degeneration Caused by a Founder Variant in C1QTNF5
利用基因编辑治疗由C1QTNF5基因创始变异引起的迟发性视网膜变性
期刊:Investigative Ophthalmology & Visual Science
影响因子:4.7
doi:10.1167/iovs.64.15.33
Li, Randa T H; Roman, Alejandro J; Sumaroka, Alexander; Stanton, Chloe M; Swider, Malgorzata; Garafalo, Alexandra V; Heon, Elise; Vincent, Ajoy; Wright, Alan F; Megaw, Roly; Aleman, Tomas S; Browning, Andrew C; Dhillon, Baljean; Cideciyan, Artur V