日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Plagl1 and Lrrc58 control mammalian body size by triggering target-directed microRNA degradation of miR-322 and miR-503

Plagl1 和 Lrrc58 通过触发 miR-322 和 miR-503 的靶向 microRNA 降解来控制哺乳动物的体型。

LaVigne, Collette A; Han, Jaeil; Zhang, He; Cho, Sihoon; Kim, Minseon; Sethia, Komal; Evers, Bret M; Acharya, Asha; Chang, Tsung-Cheng; Mendell, Joshua T

Two-Year Outcomes Following Delandistrogene Moxeparvovec Treatment in Ambulatory Patients with Duchenne Muscular Dystrophy: Phase 3 EMBARK Trial

Delandistrogene Moxeparvovec 治疗可活动杜氏肌营养不良症患者的两年疗效:3 期 EMBARK 试验

Mendell, Jerry R; Muntoni, Francesco; McDonald, Craig M; Mercuri, Eugenio M; Ciafaloni, Emma; Komaki, Hirofumi; Leon-Astudillo, Carmen; Nascimento, Andrés; Proud, Crystal; Schara-Schmidt, Ulrike; Veerapandiyan, Aravindhan; Zaidman, Craig M; Furgerson, Matthew; Ding, Kai; Singh, Preeti; Potter, Rachael; Asher, Damon R; Murphy, Alexander P; Reid, Carol; Hooper, Gregory; Torre, Carmen O; Manfrini, Marianna; Rodino-Klapac, Louise R

Mitochondrial DNA Damage in Substantia Nigra Pars Compacta Astrocytes Exacerbates Dopaminergic Neuron Loss in a 6-Hydroxydopamine Mouse Model of Parkinsonism.

黑质致密部星形胶质细胞中的线粒体 DNA 损伤加剧了 6-羟基多巴胺帕金森病小鼠模型中的多巴胺能神经元丢失。

Ayala Daniela A, Hall Grace M, Das Debanjana, Tijerina Eliana, Villagran Luisa Lopez, Khan Zaid, Paliwal Devanshi, Anand Anu, Rimer Mendell, Srinivasan Rahul

Investigation of neglected bacterial pathogens provides molecular and serological evidence of Bartonella spp. in patients with acute undifferentiated febrile illness in Villeta, Colombia

对被忽视的细菌病原体的研究提供了哥伦比亚维列塔急性不明发热性疾病患者体内巴尔通体属的分子和血清学证据。

Silva-Ramos, Carlos Ramiro; Matiz-González, J Manuel; Mendell, Nicole L; Barrero-Rubiano, C Alexander; Faccini-Martínez, Álvaro A; Cuervo, Claudia; Melby, Peter C; Aguilar, Patricia V; Cabada, Miguel M; Walker, David H; Hidalgo, Marylin

AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial.

AAV基因疗法治疗杜氏肌营养不良症:EMBARK 3期随机试验

Mendell Jerry R, Muntoni Francesco, McDonald Craig M, Mercuri Eugenio M, Ciafaloni Emma, Komaki Hirofumi, Leon-Astudillo Carmen, Nascimento Andrés, Proud Crystal, Schara-Schmidt Ulrike, Veerapandiyan Aravindhan, Zaidman Craig M, Guridi Maitea, Murphy Alexander P, Reid Carol, Wandel Christoph, Asher Damon R, Darton Eddie, Mason Stefanie, Potter Rachael A, Singh Teji, Zhang Wenfei, Fontoura Paulo, Elkins Jacob S, Rodino-Klapac Louise R

A multi-kinase inhibitor screen identifies inhibitors preserving stem-cell-like chimeric antigen receptor T cells

多激酶抑制剂筛选鉴定出能够维持干细胞样嵌合抗原受体T细胞的抑制剂

Feifei Song ,Ourania Tsahouridis ,Simone Stucchi ,Tara Walhart ,Sophie Mendell ,P Brian Hardy ,Matthew Axtman ,Shiva K R Guduru ,Thomas S K Gilbert ,Lee M Graves ,Laura E Herring ,Barbara Savoldo ,Xingcong Ma ,Mark Woodcock ,Justin J Milner ,Anastasia Ivanova ,Kenneth H Pearce ,Yang Xu ,Gianpietro Dotti

Quantitative Muscle Magnetic Resonance Outcomes in Patients With Duchenne Muscular Dystrophy: An Exploratory Analysis From the EMBARK Randomized Clinical Trial

杜氏肌营养不良症患者的定量肌肉磁共振结果:来自 EMBARK 随机临床试验的探索性分析

Vandenborne, Krista; Walter, Glenn A; Straub, Volker; Willcocks, Rebecca J; Forbes, Sean C; Mercuri, Eugenio M; Muntoni, Francesco; Ding, Kai; Ennamuri, Sravya; Reid, Carol; Murphy, Alexander P; Manfrini, Marianna; Mendell, Jerry R; Elkins, Jacob S; Rodino-Klapac, Louise R

Post-resection delivery of a TLR7/8 agonist from a biodegradable scaffold achieves immune-mediated glioblastoma clearance and protection against tumor challenge in mice

小鼠胶质母细胞瘤切除术后,通过可生物降解支架递送TLR7/8激动剂,可实现免疫介导的胶质母细胞瘤清除,并保护小鼠免受肿瘤攻击。

Elizabeth G Graham-Gurysh ,Ryan N Woodring ,Sean R Simpson ,Sophie E Mendell ,Nicole Rose Lukesh ,Erik S Pena ,Kathryn M Moore ,Luis A Ontiveros-Padilla ,Aaron T Hendricksen ,Alexandra M Lopez ,Grace L Williamson ,Connor T Murphy ,Christopher J Genito ,Kaitlyn A Hipp ,Garima Singh ,William C Zamboni ,Shawn D Hingtgen ,Peter E Fecci ,Eric M Bachelder ,Kristy M Ainslie

An ultraconserved snoRNA-like element in long noncoding RNA CRNDE promotes ribosome biogenesis and cell proliferation

长链非编码RNA CRNDE中一种超保守的snoRNA样元件促进核糖体生物合成和细胞增殖

Jong-Sun Lee ,Tu Dan ,He Zhang ,Yujing Cheng ,Frederick Rehfeld ,James Brugarolas ,Joshua T Mendell

Biodegradable nanofibrous scaffolds enhance standard of care for glioblastoma via localized targeted therapy

生物可降解纳米纤维支架通过局部靶向治疗提高胶质母细胞瘤的治疗标准

Woodring, Ryan N; Graham-Gurysh, Elizabeth G; Mendell, Sophie E; Shilling, Kevin E; Lukesh, Nicole Rose; Hipp, Katie A; Zamboni, William C; Bachelder, Eric M; Ainslie, Kristy M