Systemic delivery of AAV5, AAV8, and AAV9 packaging a C5-12-microdystrophin-FLAG expression cassette in non-human primates
在非人类灵长类动物中系统性递送包装 C5-12-microdystrophin-FLAG 表达盒的 AAV5、AAV8 和 AAV9
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2025.101411
Mengping Liu, Erica Cook, Yanshan Dai, Erich Ehlert, Francois du Plessis, Jacek Lubelski, Bogdan G Sleczka, Petia Shipkova, Zhuyin Li, Joshua Gamse, David Gordon, Leonard P Adam, Paul C Levesque, Glen B Banks