日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Author Correction: A streamlined base editor engineering strategy to reduce bystander editing

作者校正:一种简化的基础编辑器工程策略,旨在减少旁观者编辑

Valdez, Izabella; O'Connor, Ian; Patel, Divesh; Gierer, Katherine; Harrington, Jan; Ellis, Ethan; Caponetti, Stephen A; Sebra, Robert P; Valley, Hillary C; Coote, Kevin; Mense, Martin; Marro, Samuele G; Jiang, Tingting

Upregulation of a CFTR mRNA isoform has therapeutic potential for the treatment of 3' CFTR PTC variants

CFTR mRNA亚型的上调具有治疗3' CFTR PTC变异体的治疗潜力。

Allaire, Normand E; Armstrong, Matthew S; Yoon, Jae Seok; Walker, Mercy C; Bhatt, Priyanka; Harrington, Jan M; Cheng, Yi; Wong, Eric I; Mahoney, John E; Valley, Hillary C; Macadino, Caitlin M; Bihler, Hermann J; Sivachenko, Andrey Y; Cotton, Calvin U; Carulli, John P; Mense, Martin

ACE-tRNAs are a platform technology for suppressing nonsense mutations that cause cystic fibrosis.

ACE-tRNA 是一种用于抑制导致囊性纤维化的无义突变的平台技术

Ko Wooree, Porter Joseph J, Spelier Sacha, Sorensen Emily G, Bhatt Priyanka, Gabell Jeffrey T, van der Windt Isabelle, Couch Tyler, Coote Kevin, Mense Martin, Beekman Jeffrey M, Lueck John D

CFTR modulator theratyping: Current status, gaps and future directions

CFTR调节因子治疗分型:现状、差距和未来方向

Clancy, John Paul; Cotton, Calvin U; Donaldson, Scott H; Solomon, George M; VanDevanter, Donald R; Boyle, Michael P; Gentzsch, Martina; Nick, Jerry A; Illek, Beate; Wallenburg, John C; Sorscher, Eric J; Amaral, Margarida D; Beekman, Jeffrey M; Naren, Anjaparavanda P; Bridges, Robert J; Thomas, Philip J; Cutting, Garry; Rowe, Steven; Durmowicz, Anthony G; Mense, Martin; Boeck, Kris D; Skach, William; Penland, Christopher; Joseloff, Elizabeth; Bihler, Hermann; Mahoney, John; Borowitz, Drucy; Tuggle, Katherine L