日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Five-Year Extension Results of the Phase 1 START Trial of Onasemnogene Abeparvovec in Spinal Muscular Atrophy

Onasemnogene Abeparvovec治疗脊髓性肌萎缩症的1期START试验五年扩展结果

Mendell, Jerry R; Al-Zaidy, Samiah A; Lehman, Kelly J; McColly, Markus; Lowes, Linda P; Alfano, Lindsay N; Reash, Natalie F; Iammarino, Megan A; Church, Kathleen R; Kleyn, Aaron; Meriggioli, Matthew N; Shell, Richard

Anti-HMGCR myopathy may resemble limb-girdle muscular dystrophy

抗HMGCR肌病可能类似于肢带型肌营养不良症

Mohassel, Payam; Landon-Cardinal, Océane; Foley, A Reghan; Donkervoort, Sandra; Pak, Katherine S; Wahl, Colleen; Shebert, Robert T; Harper, Amy; Fequiere, Pierre; Meriggioli, Matthew; Toro, Camilo; Drachman, Daniel; Allenbach, Yves; Benveniste, Olivier; Béhin, Anthony; Eymard, Bruno; Lafôret, Pascal; Stojkovic, Tanya; Mammen, Andrew L; Bönnemann, Carsten G

Safety, tolerability, and preliminary efficacy of an IGF-1 mimetic in patients with spinal and bulbar muscular atrophy: a randomised, placebo-controlled trial

一项随机、安慰剂对照试验评估了IGF-1类似物在脊髓延髓肌萎缩症患者中的安全性、耐受性和初步疗效。

Grunseich, Christopher; Miller, Ram; Swan, Therese; Glass, David J; El Mouelhi, Mohamed; Fornaro, Mara; Petricoul, Olivier; Vostiar, Igor; Roubenoff, Ronenn; Meriggioli, Matthew N; Kokkinis, Angela; Guber, Robert D; Budron, Maher S; Vissing, John; Soraru, Gianni; Mozaffar, Tahseen; Ludolph, Albert; Kissel, John T; Fischbeck, Kenneth H

Current Treatment, Emerging Translational Therapies, and New Therapeutic Targets for Autoimmune Myasthenia Gravis

自身免疫性重症肌无力的当前治疗、新兴转化疗法和新的治疗靶点

Guptill, Jeffrey T; Soni, Madhu; Meriggioli, Matthew N

Muscle autoantibodies in myasthenia gravis: beyond diagnosis?

重症肌无力中的肌肉自身抗体:诊断之外的难题?

Meriggioli, Matthew N; Sanders, Donald B

GM-CSF-induced regulatory T cells selectively inhibit anti-acetylcholine receptor-specific immune responses in experimental myasthenia gravis

GM-CSF诱导的调节性T细胞选择性抑制实验性重症肌无力中的抗乙酰胆碱受体特异性免疫反应

Sheng, Jian Rong; Muthusamy, Thiruppathi; Prabhakar, Bellur S; Meriggioli, Matthew N

In vivo adsorption of autoantibodies in myasthenia gravis using Nanodisc-incorporated acetylcholine receptor

利用纳米盘包裹的乙酰胆碱受体在重症肌无力患者体内吸附自身抗体

Sheng, Jian Rong; Grimme, Steve; Bhattacharya, Palash; Stowell, Michael H B; Artinger, Michael; Prabahakar, Bellur S; Meriggioli, Matthew N

Autoimmune myasthenia gravis: emerging clinical and biological heterogeneity

自身免疫性重症肌无力:临床和生物学异质性的出现

Meriggioli, Matthew N; Sanders, Donald B