Pharmacokinetic, pharmacodynamic, and immunogenic rationale for optimal dosing of pegvaliase, a PEGylated bacterial enzyme, in adult patients with phenylketonuria
苯丙酮尿症成人患者中聚乙二醇化细菌酶培格伐利酶最佳剂量的药代动力学、药效学和免疫原性原理
期刊:Cts-Clinical and Translational Science
影响因子:2.8
doi:10.1111/cts.13043
Qi, Yulan; Patel, Gina; Henshaw, Joshua; Gupta, Soumi; Olbertz, Joy; Larimore, Kevin; Harding, Cary O; Merilainen, Markus; Zori, Roberto; Longo, Nicola; Burton, Barbara K; Li, Mingjin; Gu, Zhonghua; Zoog, Stephen J; Weng, Haoling H; Schweighardt, Becky