Improvements in health-related quality of life in patients with transfusion-dependent β-thalassemia after exagamglogene autotemcel
输血依赖型β-地中海贫血患者接受exagamglogene autotemcel治疗后,其健康相关生活质量得到改善。
期刊:Blood Advances
影响因子:
doi:10.1182/bloodadvances.2025016702
Fuente, Josu de la; Frangoul, Haydar; Lang, Peter; Wall, Donna; Meisel, Roland; Corbacioglu, Selim; Li, Amanda M; Shah, Ami J; Carpenter, Ben; Kwiatkowski, Janet L; Mapara, Markus Y; Liem, Robert I; Rupprecht, Joachim; Kuo, Kevin H M; Merkeley, Hayley; Algeri, Mattia; Smith, Wally; Kohli, Puja; Li, Nanxin; Rubin, Jaime; Zhang, Siyu; Hobbs, William; Locatelli, Franco