Efficient and safe correction of hemophilia A by lentiviral vector-transduced BOECs in an implantable device
利用植入式装置中慢病毒载体转导的BOECs高效安全地纠正A型血友病
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2021.10.015
Olgasi, Cristina; Borsotti, Chiara; Merlin, Simone; Bergmann, Thorsten; Bittorf, Patrick; Adewoye, Adeolu Badi; Wragg, Nicholas; Patterson, Kelcey; Calabria, Andrea; Benedicenti, Fabrizio; Cucci, Alessia; Borchiellini, Alessandra; Pollio, Berardino; Montini, Eugenio; Mazzuca, Delfina M; Zierau, Martin; Stolzing, Alexandra; Toleikis, Philip M; Braspenning, Joris; Follenzi, Antonia