日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

AAV gene therapy in companion dogs with severe hemophilia: Real-world long-term data on immunogenicity, efficacy, and quality of life

针对患有严重血友病的伴侣犬的AAV基因疗法:关于免疫原性、疗效和生活质量的真实世界长期数据

Doshi, Bhavya S; Samelson-Jones, Benjamin J; Nichols, Timothy C; Merricks, Elizabeth P; Siner, Joshua L; French, Robert A; Lee, Ben J; Arruda, Valder R; Callan, Mary Beth

Recombinant von Willebrand factor and tranexamic acid for heavy menstrual bleeding in patients with mild and moderate von Willebrand disease in the USA (VWDMin): a phase 3, open-label, randomised, crossover trial

在美国,一项针对轻度至中度血管性血友病(VWDMin)患者,采用重组血管性血友病因子和氨甲环酸治疗月经过多的3期开放标签随机交叉试验

Ragni, Margaret V; Rothenberger, Scott D; Feldman, Robert; Nance, Danielle; Leavitt, Andrew D; Malec, Lynn; Kulkarni, Roshni; Sidonio, Robert Jr; Kraut, Eric; Lasky, Joseph; Pruthi, Rajiv; Angelini, Dana; Philipp, Claire; Hwang, Nina; Wheeler, Allison P; Seaman, Craig; Machin, Nicoletta; Xavier, Frederico; Meyer, Michael; Bellissimo, Daniel; Humphreys, Gregory; Smith, Kenneth J; Merricks, Elizabeth P; Nichols, Timothy C; Ivanco, Dana; Vehec, Deborah; Koerbel, Glory; Althouse, Andrew D

Mechanisms of Foreign Body Response Mitigation by Nitric Oxide Release

一氧化氮释放缓解异物反应的机制

Taylor, James B; Malone-Povolny, Maggie J; Merricks, Elizabeth P; Wimsey, Lauren E; Soliman, Daniel; Nichols, Timothy C; Wallet, Shannon M; Maile, Robert; Schoenfisch, Mark H

Evolutionary insights into coagulation factor IX Padua and other high-specific-activity variants

对凝血因子IX Padua和其他高比活性变体的进化见解

Samelson-Jones, Benjamin J; Finn, Jonathan D; Raffini, Leslie J; Merricks, Elizabeth P; Camire, Rodney M; Nichols, Timothy C; Arruda, Valder R

Preclinical evaluation of a next-generation, subcutaneously administered, coagulation factor IX variant, dalcinonacog alfa

对新一代皮下注射凝血因子IX变体dalcinonacog alfa进行临床前评估

Nichols, Timothy C; Levy, Howard; Merricks, Elizabeth P; Raymer, Robin A; Lee, Martin L

Long-Term Accurate Continuous Glucose Biosensors via Extended Nitric Oxide Release

通过延长一氧化氮释放实现长期、精确的连续葡萄糖生物传感器

Malone-Povolny, Maggie J; Merricks, Elizabeth P; Wimsey, Lauren E; Nichols, Timothy C; Schoenfisch, Mark H

Mechanical Anisotropy Assessment in Kidney Cortex Using ARFI Peak Displacement: Preclinical Validation and Pilot In Vivo Clinical Results in Kidney Allografts

利用ARFI峰值位移评估肾皮质的力学各向异性:肾移植的临床前验证和初步体内临床试验结果

Hossain, Md Murad; Detwiler, Randal K; Chang, Emily H; Caughey, Melissa C; Fisher, Melrose W; Nichols, Timothy C; Merricks, Elizabeth P; Raymer, Robin A; Whitford, Margaret; Bellinger, Dwight A; Wimsey, Lauren E; Gallippi, Caterina M

Oral Tolerance Induction in Hemophilia B Dogs Fed with Transplastomic Lettuce

用转基因生菜喂养的B型血友病犬的口服耐受性诱导

Herzog, Roland W; Nichols, Timothy C; Su, Jin; Zhang, Bei; Sherman, Alexandra; Merricks, Elizabeth P; Raymer, Robin; Perrin, George Q; Häger, Mattias; Wiinberg, Bo; Daniell, Henry

Evaluation of engineered AAV capsids for hepatic factor IX gene transfer in murine and canine models.

在小鼠和犬模型中评估工程化 AAV 衣壳对肝因子 IX 基因转移的作用

Markusic David M, Nichols Timothy C, Merricks Elizabeth P, Palaschak Brett, Zolotukhin Irene, Marsic Damien, Zolotukhin Sergei, Srivastava Arun, Herzog Roland W

Global measurement of coagulation in plasma from normal and haemophilia dogs using a novel modified thrombin generation test - Demonstrated in vitro and ex vivo

利用一种新型改良的凝血酶生成试验,对正常犬和血友病犬血浆中的凝血功能进行整体测量——已在体外和离体实验中得到验证

Madsen, Daniel Elenius; Nichols, Timothy C; Merricks, Elizabeth P; Waters, Emily K; Wiinberg, Bo