rAAV6-microdystrophin preserves muscle function and extends lifespan in severely dystrophic mice
rAAV6-微型肌营养不良蛋白可保护重度肌营养不良小鼠的肌肉功能并延长其寿命。
期刊:Nature Medicine
影响因子:50
doi:10.1038/nm1439
Gregorevic, Paul; Allen, James M; Minami, Elina; Blankinship, Michael J; Haraguchi, Miki; Meuse, Leonard; Finn, Eric; Adams, Marvin E; Froehner, Stanley C; Murry, Charles E; Chamberlain, Jeffrey S