Cell-mediated cytotoxicity within CSF and brain parenchyma in spinal muscular atrophy unaltered by nusinersen treatment
脊髓性肌萎缩症患者脑脊液和脑实质内的细胞介导细胞毒性不受 Nusinersen 治疗的影响
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-024-48195-3
I-Na Lu, Phyllis Fung-Yi Cheung, Michael Heming, Christian Thomas, Giovanni Giglio, Markus Leo, Merve Erdemir, Timo Wirth, Simone König, Christine A Dambietz, Christina B Schroeter, Christopher Nelke, Jens T Siveke, Tobias Ruck, Luisa Klotz, Carmen Haider, Romana Höftberger, Christoph Kleinschnitz,