日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

3D Quantification of Viral Transduction Efficiency in Living Human Retinal Organoids

活体人视网膜类器官中病毒转导效率的三维定量分析

Rogler, Teresa S; Salbaum, Katja A; Brinkop, Achim T; Sonntag, Selina M; James, Rebecca; Shelton, Elijah R; Thielen, Alina; Rose, Roland; Babutzka, Sabrina; Klopstock, Thomas; Michalakis, Stylianos; Serwane, Friedhelm

Safety and vision outcomes of subretinal gene supplementation therapy in PDE6A-associated retinitis pigmentosa: a non-randomised controlled trial

视网膜下基因补充疗法治疗PDE6A相关性视网膜色素变性的安全性和视力结果:一项非随机对照试验

Reichel, Felix F; Fischer, M Dominik; Stingl, Katarina; Kuehlewein, Laura; Seitz, Immanuel; Peters, Tobias; Ziegler, Melanie; Wilhelm, Barbara; Kohl, Susanne; Weisschuh, Nicole; Martus, Peter; Seeliger, Mathias; Muehlfriedel, Regine; Paquet-Durand, Francois; Tsang, Stephen H; Bartz-Schmidt, Karl Ulrich; Ueffing, Marius; Zrenner, Eberhart; Biel, Martin; Wissinger, Bernd; Michalakis, Stylianos

CRISPR/Cas-mediated activation of genes associated with inherited retinal dystrophies in human cells for diagnostic purposes

利用 CRISPR/Cas 介导的基因编辑技术激活人类细胞中与遗传性视网膜营养不良相关的基因,以用于诊断目的

Weber, Valentin J; Reschigna, Alice; Gerhardt, Maximilian J; Heigl, Thomas; Hinrichsmeyer, Klara S; den Engel, Sander van; Otify, Dina Y; Gavrilov, Zoran; Blaser, Frank; Meneau, Isabelle; Betz, Christian; Bolz, Hanno J; Biel, Martin; Michalakis, Stylianos; Becirovic, Elvir

Investigating the Immunogenic Potential of Variations in Host Cell Protein Levels in Clinical-Grade AAV8 Products.

研究临床级 AAV8 产品中宿主细胞蛋白水平变化的免疫原性潜力

Seitz Immanuel P, Rodríguez-Bocanegra Eduardo, Bucher Kirsten, Reichel Felix F, Michalakis Stylianos, Romanovsky Dimitri, Biel Martin, Wissinger Bernd, Bartz-Schmidt Karl-Ulrich, Peters Tobias, Fischer Manuel D

Deep Learning-Based Retinal Layer Segmentation in Optical Coherence Tomography Scans of Patients with Inherited Retinal Diseases

基于深度学习的遗传性视网膜疾病患者光学相干断层扫描视网膜层分割

Eckardt, Franziska; Mittas, Robin; Horlava, Nastassya; Schiefelbein, Johannes; Asani, Ben; Michalakis, Stylianos; Gerhardt, Maximilian; Priglinger, Claudia; Keeser, Daniel; Koutsouleris, Nikolaos; Priglinger, Siegfried; Theis, Fabian; Peng, Tingying; Schworm, Benedikt

Development of a translatable gene augmentation therapy for CNGB1-retinitis pigmentosa

开发一种可转化的基因增强疗法用于治疗 CNGB1 基因突变引起的视网膜色素变性

Occelli, Laurence M; Zobel, Lena; Stoddard, Jonathan; Wagner, Johanna; Pasmanter, Nathaniel; Querubin, Janice; Renner, Lauren M; Reynaga, Rene; Winkler, Paige A; Sun, Kelian; Marinho, Luis Felipe L P; O'Riordan, Catherine R; Frederick, Amy; Lauer, Andreas; Tsang, Stephen H; Hauswirth, William W; McGill, Trevor J; Neuringer, Martha; Michalakis, Stylianos; Petersen-Jones, Simon M

Biology, Pathobiology and Gene Therapy of CNG Channel-Related Retinopathies

CNG通道相关视网膜病变的生物学、病理生物学和基因治疗

Gerhardt, Maximilian J; Priglinger, Siegfried G; Biel, Martin; Michalakis, Stylianos

CNG channel-related retinitis pigmentosa

CNG通道相关性视网膜色素变性

Gerhardt, Maximilian J; Petersen-Jones, Simon M; Michalakis, Stylianos

Suppression of SARS-CoV-2 Replication with Stabilized and Click-Chemistry Modified siRNAs

利用稳定化和点击化学修饰的siRNA抑制SARS-CoV-2复制

Traube, Franziska R; Stern, Marcel; Tölke, Annika J; Rudelius, Martina; Mejías-Pérez, Ernesto; Raddaoui, Nada; Kümmerer, Beate M; Douat, Céline; Streshnev, Filipp; Albanese, Manuel; Wratil, Paul R; Gärtner, Yasmin V; Nainytė, Milda; Giorgio, Grazia; Michalakis, Stylianos; Schneider, Sabine; Streeck, Hendrik; Müller, Markus; Keppler, Oliver T; Carell, Thomas

More than meets the eye: The role of microglia in healthy and diseased retina

眼见未必为实:小胶质细胞在健康和病变视网膜中的作用

Murenu, Elisa; Gerhardt, Maximilian-Joachim; Biel, Martin; Michalakis, Stylianos