Development of translational read-through-inducing drugs as novel therapeutic options for patients with Fanconi anemia.
开发转化阅读通读诱导药物作为范可尼贫血患者的新型治疗选择
期刊:Cell Death Discovery
影响因子:7
doi:10.1038/s41420-025-02571-0
Hristodor Anca Manuela, Cappelli Enrico, Baldisseri Elena, Valli Roberto, Montalbano Giuseppe, Micheloni Giovanni, Porta Giovanni, Frattini Annalisa, Ravera Silvia, Fioredda Francesca, Lippi Giuseppe, Dufour Carlo, Cipolli Marco, Bezzerri Valentino